Human Gene Therapy for a Synaptic Disease: X-Linked Retinoschisis (XLRS)

被引：0
|
作者：
Sieving, Paul A. [1 ]
Vijayasarathy, Camasamudram [2 ]
Ou, Jinxing [1 ]
Ziccardi, Lucia [2 ]
Chen, Shan [1 ]
Zeng, Yong [2 ]
Marangoni, Dario [2 ]
Li, Wei [1 ]
Wu, Zhijian [1 ]
Wei, Lisa L. [1 ]
Bush, Ronald A. [2 ]
机构：
[1] NEI, Bethesda, MD 20892 USA
[2] Natl Inst Deafness & Other Commun Disorders, NIH, Bethesda, MD USA
来源：
MOLECULAR THERAPY | 2015年 / 23卷
关键词：
D O I：
10.1016/S1525-0016(16)34209-5
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
600
引用
收藏
页码：S238 / S238
页数：1
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