Establishing the platform for clinical gene therapy of p47phox chronic granulomatous disease (CGD)

被引：0
|
作者：
Schejtman, A. [1 ]
Cutrim Arago Filho, W. [2 ]
Zinicola, M. [1 ]
Siler, U. [3 ]
Reichenbach, J. [3 ]
Gaspar, H. B. [1 ]
Condino-Neto, A. [2 ]
Thrasher, A. J. [1 ]
Santilli, G. [1 ]
机构：
[1] UCL, Inst Child Hlth, London, England
[2] Univ Sao Paulo, Sao Paulo, Brazil
[3] Univ Childrens Hosp Zurich, Zurich, Switzerland
来源：
HUMAN GENE THERAPY | 2016年 / 27卷 / 11期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P227
引用
收藏
页码：A114 / A115
页数：2
相关论文
共 50 条
  • [11] Correction to: Diabetes, Renal, and Cardiovascular Disease in p47phox−/− Chronic Granulomatous Disease
    Gouri P. Hule
    Journal of Clinical Immunology, 2018, 38 : 737 - 738
  • [12] Myelospecific self-inactivating gammaretroviral vectors for p47phox CGD gene therapy
    Wohlgensinger, Vital
    Brendel, Christian
    Schambach, Axel
    Grez, Manuel
    Reichenbach, Janine
    Seger, Reinhard
    Siler, Ulrich
    HUMAN GENE THERAPY, 2009, 20 (11) : 1397 - 1398
  • [13] A case of Williams Beuren syndrome with p47phox deficient chronic granulomatous disease
    Brion, J. P.
    Amblard, F.
    Martel, C.
    Mollin, M.
    Satre, V.
    Beaumel, S.
    Stasia, M. J.
    EUROPEAN JOURNAL OF CLINICAL INVESTIGATION, 2011, 41 : 47 - 48
  • [14] Disseminated Tuberculosis in a Patient with Autosomal Recessive p47phox Chronic Granulomatous Disease
    Ximena León-Lara
    Alejandro Campos-Murguía
    Pablo León-Cabral
    Andrea Tello-Mercado
    Noel Salgado-Nesme
    Jesús Delgado de la Mora
    Stéphanie Boisson- Dupuis
    Jacinta Bustamante
    Lizbeth Blancas-Galicia
    Journal of Clinical Immunology, 2021, 41 : 1417 - 1419
  • [15] Disseminated Tuberculosis in a Patient with Autosomal Recessive p47phox Chronic Granulomatous Disease
    Leon-Lara, Ximena
    Campos-Murguia, Alejandro
    Leon-Cabral, Pablo
    Tello-Mercado, Andrea
    Salgado-Nesme, Noel
    de la Mora, Jesus Delgado
    Dupuis, Stephanie Boisson-
    Bustamante, Jacinta
    Blancas-Galicia, Lizbeth
    JOURNAL OF CLINICAL IMMUNOLOGY, 2021, 41 (06) : 1417 - 1419
  • [16] Development of a pCCLChim Lentiviral Vector for Gene Therapy of Patients with Chronic Granulomatous Disease (CGD) due to p47-phox Deficiency
    Aragao-Filho, Walmir Cutrim
    Shejtman, Andrea
    Zinicola, Marta
    Siler, Ulrich
    Reichenbach, Janine
    Gaspar, H. B.
    Thrasher, Adrian
    Santilli, Giorgia
    Condino-Neto, Antonio
    JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2017, 139 (02) : AB186 - AB186
  • [17] Chronic Granulomatous Disease Caused by a Deficiency in p47phox Mimicking Crohn's Disease
    Huang, Jeannie S.
    Noack, Deborah
    Rae, Julie
    Ellis, Beverly A.
    Newbury, Robert
    Pong, Alice L.
    Lavine, Joel E.
    Curnutte, John T.
    Bastian, John
    CLINICAL GASTROENTEROLOGY AND HEPATOLOGY, 2004, 2 (08) : 690 - 695
  • [18] Lentiviral vector for p47phox gene therapy
    Haenseler, W.
    Brendel, C.
    Santili, G.
    James, W.
    Cowley, S.
    Thrasher, A.
    Grez, M.
    Reichenbach, J.
    Siler, U.
    HUMAN GENE THERAPY, 2013, 24 (12) : A75 - A76
  • [19] Correction of p47-phox deficient Chronic Granulomatous Disease by lentiviral gene therapy
    Schejtman, Andrea
    Cutrim Aragao Filho, W.
    Clare, S.
    Weisser, M.
    Zinicola, M.
    Booth, C.
    Burns, S. O.
    Siler, U.
    Reichenbach, J.
    Gaspar, H. B.
    Thomas, D.
    Condino-Neto, A.
    Thrasher, A. J.
    Santilli, G.
    HUMAN GENE THERAPY, 2018, 29 (07) : A12 - A12
  • [20] RAPID DETECTION OF INTRACELLULAR P47PHOX AND P67PHOX BY FLOW CYTOMERY IN PATIENTS WITH CHRONIC GRANULOMATOUS DISEASE
    Wada, T.
    Muraoka, M.
    Toma, T.
    Shigemura, T.
    Agematsu, K.
    Moriuchi, H.
    Ohara, O.
    Morio, T.
    Yachie, A.
    JOURNAL OF CLINICAL IMMUNOLOGY, 2012, 32 : 101 - 101
12345