IDENTIFICATION OF EFFICACIOUS F508DEL CFTR CORRECTORS USING A NOVEL HOMOLOGY MODEL
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作者:
Aller, S.
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Univ Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USAUniv Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USA
Aller, S.
[1
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Tang, L.
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Univ Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USAUniv Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USA
Tang, L.
[1
]
Rajpur, J.
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Univ Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USAUniv Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USA
Rajpur, J.
[1
]
Sloane, P.
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Univ Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USAUniv Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USA
Sloane, P.
[1
]
Sorscher, E. J.
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Univ Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USAUniv Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USA
Sorscher, E. J.
[1
]
Rowe, S. M.
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Univ Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USAUniv Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USA
Rowe, S. M.
[1
]
机构:
[1] Univ Alabama Birmingham, James Fleming Cyst Fibrosis Ctr, Birmingham, AL USA
机构:
Univ Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Manchester Acad Hlth Sci Ctr, Manchester, Lancs, England
St James Univ Hosp, Leeds Teaching Hosp NHS Trust, Beckett St, Leeds LS9 7TF, W Yorkshire, EnglandUniv Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Gamaletsou, Maria N.
Hayes, Gemma
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机构:
Univ Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Manchester Acad Hlth Sci Ctr, Manchester, Lancs, EnglandUniv Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Hayes, Gemma
Harris, Chris
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机构:
Univ Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Manchester Acad Hlth Sci Ctr, Manchester, Lancs, EnglandUniv Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Harris, Chris
Brock, Joanna
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Cent Manchester Univ Hosp NHS Fdn Trust, St Marys Hosp, Manchester Ctr Genom Med, Genom Diagnost Lab, Manchester, Lancs, EnglandUniv Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Brock, Joanna
Muldoon, Eavan G.
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机构:
Univ Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Manchester Acad Hlth Sci Ctr, Manchester, Lancs, EnglandUniv Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Muldoon, Eavan G.
Denning, David W.
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Univ Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
Manchester Acad Hlth Sci Ctr, Manchester, Lancs, EnglandUniv Manchester, Univ Hosp South Manchester, Natl Aspergillosis Ctr, Manchester, Lancs, England
机构:
FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
Pregel, M.
DeVit, M.
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FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
DeVit, M.
Fleming, J.
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FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
Fleming, J.
Elbaum, D.
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FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
Elbaum, D.
Balch, W.
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机构:
Scripps Res Inst, Dept Cell Biol, La Jolla, CA 92037 USA
Scripps Res Inst, Inst Childhood & Neglected Dis, La Jolla, CA 92037 USAFoldRx Pharmaceut, Cambridge, MA USA
Balch, W.
Pedemonte, N.
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机构:
Ist Giannina Gaslini, Genet Mol Lab, I-16148 Genoa, ItalyFoldRx Pharmaceut, Cambridge, MA USA
Pedemonte, N.
Galietta, L. J.
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机构:
Ist Giannina Gaslini, Genet Mol Lab, I-16148 Genoa, ItalyFoldRx Pharmaceut, Cambridge, MA USA
Galietta, L. J.
Rutkowski, J.
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FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
Rutkowski, J.
Weigel, C.
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机构:
FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
Weigel, C.
DesRosiers, R.
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机构:
FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
DesRosiers, R.
Liang, F.
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机构:
FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
Liang, F.
Eskin, J.
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机构:
FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
Eskin, J.
Li, C.
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FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
Li, C.
Bulawa, C.
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FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA
Bulawa, C.
Labaudiniere, R.
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FoldRx Pharmaceut, Cambridge, MA USAFoldRx Pharmaceut, Cambridge, MA USA