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- [42] Liver-Directed Gene Therapy for Mucopolysaccharidosis Type I (MPS I)MOLECULAR THERAPY, 2012, 20 : S123 - S124Gurda, Brittney L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USABell, Peter论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USAWang, Ping论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathol & Med Genet, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USAZhu, Yanqing论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USAO'Donnell, Patty论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathol & Med Genet, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USAVandenberghe, Luk H.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Ophthalmol, Kirlcy Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USACalcedo, Roberto论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USASanmiguel, Julio论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USAHaskins, Mark E.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathol & Med Genet, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USAWilson, James M.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA
- [43] Helper-dependent adenoviral vectors for liver-directed gene therapyHUMAN MOLECULAR GENETICS, 2011, 20 : R7 - R13Brunetti-Pierri, Nicola论文数: 0 引用数: 0 h-index: 0机构: Univ Naples Federico II, Dept Pediat, I-80131 Naples, Italy Telethon Inst Genet & Med, I-80131 Naples, Italy Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USANg, Philip论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
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Therapy, I-20132 Milan, Italy Univ Vita Salute San Raffaele, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyDella Valle, Patrizia论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Coagulat Serv, I-20132 Milan, Italy Ist Sci San Raffaele, Thrombosis Res Unit, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalySanvito, Francesca论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Dept Oncol, Pathol Unit, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalySergi, Lucia Sergi论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyGallina, Pierangela论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyBenedicenti, Fabrizio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyBellinger, Dwight论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Dept Pathol, Chapel Hill, NC 27599 USA Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyRaymer, Robin论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Dept Pathol, Chapel Hill, NC 27599 USA Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyMerricks, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Dept Pathol, Chapel Hill, NC 27599 USA Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyBellintani, Francesca论文数: 0 引用数: 0 h-index: 0机构: MolMed SpA, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyMartin, Samia论文数: 0 引用数: 0 h-index: 0机构: Genethon, F-91000 Evry, France Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyDoglioni, Claudio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Dept Oncol, Pathol Unit, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyD'Angelo, Armando论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Coagulat Serv, I-20132 Milan, Italy Ist Sci San Raffaele, Thrombosis Res Unit, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyVandenDriessche, Thierry论文数: 0 引用数: 0 h-index: 0机构: Free Univ Brussels, Dept Gene Therapy & Regenerat Med, B-1050 Brussels, Belgium Univ Leuven, Ctr Mol & Vasc Biol, Dept Cardiovasc Sci, B-3000 Louvain, Belgium Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyChuah, Marinee K.论文数: 0 引用数: 0 h-index: 0机构: Free Univ Brussels, Dept Gene Therapy & Regenerat Med, B-1050 Brussels, Belgium Univ Leuven, Ctr Mol & Vasc Biol, Dept Cardiovasc Sci, B-3000 Louvain, Belgium Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalySchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Tumor Dis, Dept Translat Oncol, D-69120 Heidelberg, Germany German Canc Res Ctr, D-69120 Heidelberg, Germany Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyNichols, Timothy论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Dept Pathol, Chapel Hill, NC 27599 USA Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyMontini, Eugenio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, ItalyNaldini, Luigi论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy Univ Vita Salute San Raffaele, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy
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- [47] Recent advances in liver-directed gene therapy: implications for the treatment of dyslipidemiaCURRENT OPINION IN LIPIDOLOGY, 2000, 11 (02) : 179 - 186Oka, K论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Texas Med Ctr, Dept Mol & Cellular Biol, Houston, TX 77030 USADavis, AR论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Texas Med Ctr, Dept Mol & Cellular Biol, Houston, TX 77030 USAChan, L论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Texas Med Ctr, Dept Mol & Cellular Biol, Houston, TX 77030 USA
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