AAV-Mediated Direct Somatic Genetic Correction of Epidermolysis Bullosa

被引:0
|
作者
Melo, Sandra [1 ]
Lisowski, Leszek [2 ,3 ]
Bashkirova, Lisa [1 ]
Kay, Mark A. [2 ,3 ]
Oro, Anthony E. [1 ]
机构
[1] Stanford Univ, Dept Dermatol, Sch Med, Stanford, CA 94305 USA
[2] Stanford Univ, Dept Pediat, Sch Med, Stanford, CA 94305 USA
[3] Stanford Univ, Dept Genet, Sch Med, Stanford, CA 94305 USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
277
引用
收藏
页码:S106 / S106
页数:1
相关论文
共 50 条
  • [41] Direct Costs of Epidermolysis Bullosa by Disease Severity
    Flannery, Darragh
    Doyle, Claire
    Hickey, Sinead
    Aherne, Fiona
    Kennan, Avril
    ACTA DERMATO-VENEREOLOGICA, 2020, 100 : 1 - 2
  • [42] Risk assessment of AAV-Mediated gene repair
    Gellhaus, Katharina
    Cornu, Tatjana
    Cathomen, Toni
    HUMAN GENE THERAPY, 2007, 18 (10) : 971 - 971
  • [43] Optimization of efficacy in AAV-mediated siRNA expression
    Mzukami, H.
    Urabe, M.
    Tsukahara, T.
    Kume, A.
    Ozawa, K.
    HUMAN GENE THERAPY, 2011, 22 (10) : A104 - A105
  • [44] AAV-mediated gene transfer of FKRP in mice
    Gicquel, Evelyne
    Maizonnier, Natacha
    Richard, Isabelle
    HUMAN GENE THERAPY, 2016, 27 (07) : A12 - A13
  • [45] AAV-mediated gene therapy of Pompe disease
    Ziegler, RJ
    Bercury, S
    Armentaro, D
    Raben, N
    Cheng, SH
    NEUROMUSCULAR DISORDERS, 2005, 15 (9-10) : 713 - 713
  • [46] Characterization of AAV-mediated dorsal root ganglionopathy
    Buss, Nicholas
    Lanigan, Lisa
    Zeller, Jillynne
    Cissell, Derek
    Metea, Monica
    Adams, Eric
    Higgins, Mikayla
    Kim, Kwi Hye
    Budzynski, Ewa
    Yang, Lin
    Liu, Ye
    Butt, Mark
    Danos, Olivier
    Fiscella, Michele
    MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2022, 24 : 342 - 354
  • [47] AAV-mediated gene transfer for retinal diseases
    Allocca, Mariacarmela
    Tessitore, Alessandra
    Cotugno, Gabriella
    Auricchio, Alberto
    EXPERT OPINION ON BIOLOGICAL THERAPY, 2006, 6 (12) : 1279 - 1294
  • [48] Immunology of AAV-mediated gene transfer in the eye
    Willett, Keiman
    Bennett, Jean
    FRONTIERS IN IMMUNOLOGY, 2013, 4
  • [49] In vivo AAV-mediated genetic engineering of white and brown adipose tissue in adult mice
    Jimenez, V.
    Munoz, S.
    Casana, E.
    Mallol, C.
    Elias, I.
    Jambrina, C.
    Ribera, A.
    Ferre, T.
    Franckhauser, S.
    Bosch, F.
    HUMAN GENE THERAPY, 2013, 24 (12) : A134 - A134
  • [50] IgM-mediated epidermolysis bullosa acquisita
    Suchniak, JM
    Diaz, LA
    Lin, MS
    Fairley, JA
    ARCHIVES OF DERMATOLOGY, 2002, 138 (10) : 1385 - 1386