Preclinical studies of WVE-210201, an investigational stereopure antisense oligonucleotide in development for the treatment of patients with duchenne muscular dystrophy (DMD)

被引：1
|
作者：
Panzara, M. [1 ]
Zhang, J. [2 ]
Rinaldi, C. [3 ]
McClorey, G. [3 ]
Bowman, K. [2 ]
Butler, D. [2 ]
Dodart, J. [2 ]
Frank-Kamenetsky, M. [2 ]
Iwamoto, N. [2 ]
Kothari, N. [2 ]
Lu, G. [2 ]
Mathieu, S. [2 ]
M, M. [1 ]
Melkonian, M. [2 ]
Menon, S. [2 ]
Standley, S. [2 ]
Yang, H. [2 ]
Zhong, Z. [2 ]
Wood, M. [3 ]
Vargeese, C. [2 ]
机构：
[1] WAVE Life Sci, Neurol Franchise, Cambridge, MA USA
[2] WAVE Life Sci, Drug Discovery, Cambridge, MA USA
[3] Univ Oxford, Physiol Anat & Genet, Oxford, England
来源：
JOURNAL OF THE NEUROLOGICAL SCIENCES | 2017年 / 381卷
关键词：
D O I：
10.1016/j.jns.2017.08.791
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
763
引用
收藏
页码：277 / 278
页数：2
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