Intraspinal Stem Cell Transplantation in Amyotrophic Lateral Sclerosis: A Phase I Safety Trial, Technical Note, and Lumbar Safety Outcomes COMMENTS

被引:0
|
作者
Liu, Charles Y.
Deftereos, Spyros
机构
关键词
D O I
暂无
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
引用
收藏
页码:416 / 416
页数:1
相关论文
共 50 条
  • [21] Completion and Outcomes of a Phase 1 Intraspinal Stem Cell Transplantation Trial for ALS
    Feldman, Eva L.
    Boulis, Nicholas M.
    Johe, Karl
    Rutkove, Seward B.
    Federici, Thais
    Polak, Meraida
    Kelly, Crystal
    Glass, Jonathan D.
    ANNALS OF NEUROLOGY, 2012, 72 : S127 - S128
  • [22] Safety and tolerability of Triumeq in amyotrophic lateral sclerosis: the Lighthouse trial
    Gold, Julian
    Rowe, Dominic B.
    Kiernan, Matthew C.
    Vucic, Steve
    Mathers, Susan
    Van Eijk, Ruben P. A.
    Nath, Avindra
    Montojo, Marta Garcia
    Norato, Gina
    Santamaria, Ulisses A.
    Rogers, Mary-Louise
    Malaspina, Andrea
    Lombardi, Vittoria
    Mehta, Puja R.
    Westeneng, Henk-Jan
    Van Den Berg, Leonard H.
    Al-Chalabi, Ammar
    AMYOTROPHIC LATERAL SCLEROSIS AND FRONTOTEMPORAL DEGENERATION, 2019, 20 (7-8) : 595 - 604
  • [23] Intraspinal delivery of bone marrow stromal cell-derived neural stem cells in patients with amyotrophic lateral sclerosis: A safety and feasibility study
    Nafissi, Shahriar
    Kazemi, Hadi
    Tiraihi, Taki
    Beladi-Moghadam, Nahid
    Faghihzadeh, Soghrat
    Faghihzadeh, Elham
    Yadegarynia, Davoud
    Sadeghi, Mostafa
    Chamani-Tabriz, Leili
    Khanfakhraei, Abdollah
    Taheri, Taher
    JOURNAL OF THE NEUROLOGICAL SCIENCES, 2016, 362 : 174 - 181
  • [24] Human Fetal Neural Stem Cell Transplantation for ALS: A Phase I Safety Trial
    Federici, T.
    Riley, J.
    Johe, K.
    Freeman, T.
    Feldman, E.
    Glass, J.
    Boulis, N.
    CELL TRANSPLANTATION, 2010, 19 (03) : 338 - 339
  • [25] Safety, phase I/II study with intrathecal and intravenous injection of mesenchymal stem cells in patients with multiple sclerosis and amyotrophic lateral sclerosis
    Karussis, Dimitrios
    Karageorgiou, Clementine
    Gowda-Kurkalli, Basan
    Vaknin-Dembinsky, Adi
    Kassis, Ibrahim
    Gkortzolidis, George
    Papageorgiou, Helen
    Stavropoulou, Ekaterini
    Petrou, Panayiota
    Ben-Hur, Tamir
    Slavin, Shimon
    MULTIPLE SCLEROSIS, 2008, 14 : S21 - S21
  • [26] Results from Phase I Clinical Trial with Intraspinal Injection of Neural Stem Cells in Amyotrophic Lateral Sclerosis: A Long-Term Outcome
    Mazzini, Letizia
    Gelati, Maurizio
    Profico, Daniela Celeste
    Soraru, Gianni
    Ferrari, Daniela
    Copetti, Massimiliano
    Muzi, Gianmarco
    Ricciolini, Claudia
    Carletti, Sandro
    Giorgi, Cesare
    Spera, Cristina
    Frondizi, Domenico
    Masiero, Stefano
    Stecco, Alessandro
    Cisari, Carlo
    Bersano, Enrica
    De Marchi, Fabiola
    Sarnelli, Maria Francesca
    Querin, Giorgia
    Cantello, Roberto
    Petruzzelli, Francesco
    Maglione, Annamaria
    Zalfa, Cristina
    Binda, Elena
    Visioli, Alberto
    Trombetta, Domenico
    Torres, Barbara
    Bernardini, Laura
    Gaiani, Alessandra
    Massara, Maurilio
    Paolucci, Silvia
    Boulis, Nicholas M.
    Vescovi, Angelo L.
    STEM CELLS TRANSLATIONAL MEDICINE, 2019, 8 (09) : 887 - 897
  • [27] Safety and tolerability of tegoprubart in patients with amyotrophic lateral sclerosis: A Phase 2A clinical trial
    Perrin, Steven
    Ladha, Shafeeq
    Maragakis, Nicholas
    Rivner, Michael H.
    Katz, Jonathan
    Genge, Angela
    Olney, Nicholas
    Lange, Dale
    Heitzman, Daragh
    Bodkin, Cynthia
    Jawdat, Omar
    Goyal, Namita A.
    Bornstein, Jeffrey D.
    Mak, Carmen
    Appel, Stanley H.
    Paganoni, Sabrina
    PLOS MEDICINE, 2024, 21 (10)
  • [28] Phase IIa trial of fingolimod for amyotrophic lateral sclerosis demonstrates acceptable acute safety and tolerability
    Berry, James D.
    Paganoni, Sabrina
    Atassi, Nazem
    Macklin, Eric A.
    Goyal, Namita
    Rivner, Michael
    Simpson, Ericka
    Appel, Stanley
    Grasso, Daniela L.
    Mejia, Nicte I.
    Mateen, Farrah
    Gill, Alan
    Vieira, Fernando
    Tassinari, Valerie
    Perrin, Steven
    MUSCLE & NERVE, 2017, 56 (06) : 1077 - 1084
  • [29] Safety and outcomes of percutaneous endoscopic gastrostomy in patients with amyotrophic lateral sclerosis
    Randall, Charles
    Liu, Anson
    Taboada, Carlo
    Havranek, Russell
    Jackson, Carlayne
    Melo, Jairo
    Asgasi, Sharon
    Jacobs, Carleigh
    Ford, Janet
    AMERICAN JOURNAL OF GASTROENTEROLOGY, 2006, 101 (09): : S406 - S406
  • [30] Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis, A Randomized Clinical Trial
    Paganoni, Sabrina
    Fournier, Christina N.
    Macklin, Eric A.
    Chibnik, Lori B.
    Quintana, Melanie
    Saville, Benjamin R.
    Detry, Michelle A.
    Vestrucci, Matteo
    Marion, Joe
    Mcglothlin, Anna
    Ajroud-Driss, Senda
    Chase, Marianne
    Pothier, Lindsay
    Harkey, Brittney A.
    Yu, Hong
    Sherman, Alexander V.
    Shefner, Jeremy M.
    Hall, Meghan
    Kittle, Gale
    Berry, James D.
    Babu, Suma
    Andrews, Jinsy
    Dagostino, Derek
    Tustison, Eric
    Giacomelli, Elisa
    Scirocco, Erica
    Alameda, Gustavo
    Locatelli, Eduardo
    Ho, Doreen
    Quick, Adam
    Katz, Jonathan
    Heitzman, Daragh
    Appel, Stanley H.
    Shroff, Sheetal
    Felice, Kevin
    Maragakis, Nicholas J.
    Simmons, Zachary
    Miller, Timothy M.
    Olney, Nicholas
    Weiss, Michael D.
    Goutman, Stephen A.
    Fernandes, Joseph Americo
    Jawdat, Omar
    Owegi, Margaret Ayo
    Foster, Laura A.
    Vu, Tuan
    Ilieva, Hristelina
    Newman, Daniel S.
    Arcila-Londono, Ximena
    Jackson, Carlayne E.
    JAMA NETWORK OPEN, 2025, 8 (02)