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- [21] B Cell Reconstitution after Gene Therapy in Patients with Wiskott Aldrich Syndrome and Comparison with Mismatched Allogeneic Hematopoietic Stem Cell TransplantationBLOOD, 2015, 126 (23)论文数: 引用数: h-index:机构:Roudaut, Cecile论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, FranceGabrion, Aurelie论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, FranceCaccavelli, Laure论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, FranceTouzot, Fabien论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, France Univ Paris 05, Sorbonne Paris Cite, IMAGINE Inst, Paris, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, FranceNeven, Benedicte论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Necker Enfants Malad, Pediat Hematol Immunol & Rhumatol Dept, Paris, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, FranceMoshous, Despina论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Necker Enfants Malad, Pediat Hematol Immunol & Rhumatol Dept, Paris, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, FranceMahlaoui, Nizar论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Necker Enfants Malad, Paris 15, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, FranceClave, Emmanuel论文数: 0 引用数: 0 h-index: 0机构: Hop St Louis, AP HP, INSERM, UMR 1160, Paris, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, FranceToubert, Antoine论文数: 0 引用数: 0 h-index: 0机构: Hop St Louis, AP HP, INSERM, UMR 1160, Paris, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, FranceFischer, Alain论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 05, Hop Necker Enfants Malad, AP HP, Serv Immunol & Hematol Pediat,CEREDIH, Paris, France Hop Univ Necker Enfants Malad, Biotherapy Dept, Paris, France论文数: 引用数: h-index:机构:
- [22] Gene Therapy for Wiskott-Aldrich SyndromeCURRENT GENE THERAPY, 2014, 14 (06) : 413 - 421Bosticardo, Marita论文数: 0 引用数: 0 h-index: 0机构: IRCCS, San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy TIGET, Milan, Italy IRCCS, San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy TIGET, Milan, ItalyFerrua, Francesca论文数: 0 引用数: 0 h-index: 0机构: IRCCS, San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy TIGET, Milan, Italy IRCCS, San Raffaele Sci Inst, Pediat Immunohematol & Bone Marrow Transplantat U, Milan, Italy IRCCS, San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy TIGET, Milan, ItalyCavazzana, Marina论文数: 0 引用数: 0 h-index: 0机构: Necker Childrens Hosp, AP HP, Biotherapy Dept, Paris, France Hosp Univ Ouest, AP HP, Paris INSERM, Biotherapy Clin Invest Ctr, Paris, France Paris Descartes Sorbonne Paris Cite Univ, Imagine Inst Paris, Paris, France IRCCS, San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy TIGET, Milan, ItalyAiuti, Alessandro论文数: 0 引用数: 0 h-index: 0机构: IRCCS, San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy TIGET, Milan, Italy IRCCS, San Raffaele Sci Inst, Pediat Immunohematol & Bone Marrow Transplantat U, Milan, Italy Univ Roma Tor Vergata, Dept Syst Med, Rome, Italy IRCCS, San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy TIGET, Milan, Italy
- [23] Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndromeNATURE MEDICINE, 2022, 28 (01) : 71 - +Magnani, A.论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, France Grp Hosp Univ Paris Ctr, AP HP, Biotherapy Clin Invest Ctr, INSERM CIC 1416, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceSemeraro, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP,Clin Invest Ctr CIC 1419, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceAdam, F.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, UMR S1176, INSERM, Le Kremlin Bicetre, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceBooth, C.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Dept Paediat Immunol, London, England UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, London, England Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceDupre, L.论文数: 0 引用数: 0 h-index: 0机构: Toulouse III Paul Sabatier Univ, Toulouse Inst Infect & Inflammatory Dis INFINITy, CNRS, INSERM, Toulouse, France Ludwig Boltzmann Inst Rare & Undiagnosed Dis, Vienna, Austria Med Univ Vienna, Dept Dermatol, Vienna, Austria Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceMorris, E. C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Immun & Transplantat, London, England Royal Free London Hosp NHS Fdn Trust, Dept Immunol, London, England Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, France论文数: 引用数: h-index:机构:Roudaut, C.论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, France Grp Hosp Univ Paris Ctr, AP HP, Biotherapy Clin Invest Ctr, INSERM CIC 1416, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, France论文数: 引用数: h-index:机构:Toubert, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, INSERM U1160, EMiLy, Inst Rech St Louis, Paris, France Hop St Louis, AP HP, Lab Immunol & Histocompatibilite, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceClave, E.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, INSERM U1160, EMiLy, Inst Rech St Louis, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceAbdo, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 05, Inst Necker Enfants Malad INEM, INSERM U1151, Sorbonne Cite, Paris, France Necker Enfants Malad Univ Hosp, AP PH, Lab Oncohematol, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceGorochov, G.论文数: 0 引用数: 0 h-index: 0机构: Grp Hosp Pitie Salpetriere, AP HP, Dept Immunol, Paris, France Sorbonne Univ, Ctr Immunol & Malad Infect Paris CIMI Paris, INSERM, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FrancePetermann, R.论文数: 0 引用数: 0 h-index: 0机构: INTS, Platelet Immunol Dept, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceGuiot, M.论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceMiyara, M.论文数: 0 引用数: 0 h-index: 0机构: Grp Hosp Pitie Salpetriere, AP HP, Dept Immunol, Paris, France Sorbonne Univ, Ctr Immunol & Malad Infect Paris CIMI Paris, INSERM, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceMoshous, D.论文数: 0 引用数: 0 h-index: 0机构: Necker Enfants Malad Univ Hosp, AP HP, Dept Pediat Immunol Hematol & Rheumatol, Paris, France Univ Paris Ctr, Imagine Inst, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceMagrin, E.论文数: 0 引用数: 0 h-index: 0机构: Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, France Grp Hosp Univ Paris Ctr, AP HP, Biotherapy Clin Invest Ctr, INSERM CIC 1416, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceDenis, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Imagine Inst, Human Lymphohematopoiesis Lab, INSERM,UMR 1163, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceSuarez, F.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Ctr, Imagine Inst, Paris, France Ctr Univ Paris, Hop Necker Enfants Malad, AP HP, Serv Hematol Adultes, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceLagresle, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Imagine Inst, Human Lymphohematopoiesis Lab, INSERM,UMR 1163, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceRoche, A. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Med, Dept Microbiol, Philadelphia, PA 19104 USA Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceEverett, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Med, Dept Microbiol, Philadelphia, PA 19104 USA Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceTrinquand, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 05, Inst Necker Enfants Malad INEM, INSERM U1151, Sorbonne Cite, Paris, France Necker Enfants Malad Univ Hosp, AP PH, Lab Oncohematol, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceGuisset, M.论文数: 0 引用数: 0 h-index: 0机构: Toulouse III Paul Sabatier Univ, Toulouse Inst Infect & Inflammatory Dis INFINITy, CNRS, INSERM, Toulouse, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceBayford, J. Xu论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Dept Paediat Immunol, London, England Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceHacein-Bey-Abina, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Unite Technol Chim & Biol Sante, INSERM, CNRS, Paris, France Hop Kremlin Bicetre, Grp Hosp Univ Paris Sud, AP HP, Clin Immunol Lab, Le Kremlin Bicetre, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceKauskot, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, UMR S1176, INSERM, Le Kremlin Bicetre, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceElfeky, R.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Dept Paediat Immunol, London, England Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceRivat, C.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Dept Paediat Immunol, London, England Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceAbbas, S.论文数: 0 引用数: 0 h-index: 0机构: Genethon, Evry, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceGaspar, H. B.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Dept Paediat Immunol, London, England Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceMacintyre, E.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 05, Inst Necker Enfants Malad INEM, INSERM U1151, Sorbonne Cite, Paris, France Necker Enfants Malad Univ Hosp, AP PH, Lab Oncohematol, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FrancePicard, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Ctr, Imagine Inst, Paris, France Necker Enfants Malad Univ Hosp, AP HP, Study Ctr Primary Immunodeficiencies, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceBushman, F. D.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Med, Dept Microbiol, Philadelphia, PA 19104 USA Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceGaly, A.论文数: 0 引用数: 0 h-index: 0机构: Genethon, Evry, France Univ Paris Saclay, Univ Evry, Integrare Res Unit UMRS951, INSERM,Genethon, Evry, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceFischer, A.论文数: 0 引用数: 0 h-index: 0机构: Necker Enfants Malad Univ Hosp, AP HP, Dept Pediat Immunol Hematol & Rheumatol, Paris, France Univ Paris Ctr, Imagine Inst, Paris, France Coll France, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceSix, E.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Imagine Inst, Human Lymphohematopoiesis Lab, INSERM,UMR 1163, Paris, France Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, FranceThrasher, A. J.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Dept Paediat Immunol, London, England UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, London, England Hop Univ Necker Enfants Malad, Grp Hosp Paris Ctr, AP HP, Dept Biotherapy, Paris, France论文数: 引用数: h-index:机构:
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- [27] Targeted gene correction of human hematopoietic stem cells for the treatment of Wiskott - Aldrich SyndromeNature Communications, 11Rajeev Rai论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthMarianna Romito论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthElizabeth Rivers论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthGiandomenico Turchiano论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthGeorges Blattner论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthWinston Vetharoy论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthDariusz Ladon论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthGeoffroy Andrieux论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthFang Zhang论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthMarta Zinicola论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthDiego Leon-Rico论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthGiorgia Santilli论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthAdrian J. Thrasher论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child HealthAlessia Cavazza论文数: 0 引用数: 0 h-index: 0机构: University College London,Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child Health
- [28] Targeted gene correction of human hematopoietic stem cells for the treatment of Wiskott - Aldrich SyndromeNATURE COMMUNICATIONS, 2020, 11 (01)Rai, Rajeev论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandRomito, Marianna论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandRivers, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandTurchiano, Giandomenico论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandBlattner, Georges论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandVetharoy, Winston论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandLadon, Dariusz论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Children NHS Fdn Trust, SIHMDS Acquired Genom, Great Ormond St, London WC1N 3JH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandAndrieux, Geoffroy论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Inst Med Bioinformat & Syst Med, 26 Stefan Meier Str, D-79104 Freiburg, Germany UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandZhang, Fang论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandZinicola, Marta论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandLeon-Rico, Diego论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandSantilli, Giorgia论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandThrasher, Adrian J.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, EnglandCavazza, Alessia论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Res & Teaching Dept, 30 Guilford St, London WC1N 1EH, England
- [29] Gene therapy for Wiskott-Aldrich syndromeEXPERT OPINION ON ORPHAN DRUGS, 2013, 1 (09): : 705 - 715Witzel, Maximilian Georg Wolfgang论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dr von Hauner Childrens Hosp, Munich, Germany Univ Munich, Dr von Hauner Childrens Hosp, Munich, GermanyBraun, Christian Joerg论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dr von Hauner Childrens Hosp, Munich, Germany Univ Munich, Dr von Hauner Childrens Hosp, Munich, GermanyBoztug, Kaan论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, Munich, Germany Univ Munich, Dr von Hauner Childrens Hosp, Munich, GermanyKlein, Christoph论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dr von Hauner Childrens Hosp, Munich, Germany Univ Munich, Dr von Hauner Childrens Hosp, Munich, Germany
- [30] Gene therapy for the Wiskott-Aldrich syndromeCURRENT OPINION IN ALLERGY AND CLINICAL IMMUNOLOGY, 2011, 11 (06) : 545 - 550Galy, Anne论文数: 0 引用数: 0 h-index: 0机构: INSERM, U951, Evry, France INSERM, U951, Evry, FranceThrasher, Adrian J.论文数: 0 引用数: 0 h-index: 0机构: UCL Inst Child Hlth, Ctr Immunodeficiency, London, England Great Ormond St Hosp NHS Trust, London, England INSERM, U951, Evry, France