COMBINED ENZYME-REPLACEMENT AND SUBSTRATE-REDUCTION THERAPIES IN GAUCHER DISEASE TYPE II/III

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作者
Gautschi, M. [1 ]
Nava, E. [2 ]
Simonetti, Goeggel B. [2 ]
Nuoffer, J. M. [3 ]
机构
[1] Univ Child Hosp, Interdiscipl Metab Unit, Bern, Switzerland
[2] Univ Child Hosp, Neuropediat Unit, Bern, Switzerland
[3] Univ Hosp Bern, Inst Clin Chem, CH-3010 Bern, Switzerland
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R5 [内科学];
学科分类号
1002 ; 100201 ;
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页码:S200 / S200
页数:1
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