共 50 条
- [21] Mapping brain networks in MPS I mice and their restoration following gene therapySCIENTIFIC REPORTS, 2023, 13 (01):Zhu, Wei论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USA Univ Minnesota, Dept Radiol, Minneapolis, MN 55455 USA Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USAOu, Li论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Dept Pediat, Minneapolis, MN 55455 USA Genemag Biosci, Media, PA 19063 USA Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USAZhang, Lin论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Div Biostat, Minneapolis, MN 55455 USA Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USAClark, Isaac H.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Biomed Engn Grad Program, Minneapolis, MN 55455 USA Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USAZhang, Ying论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minnesota Supercomputing Inst, Minneapolis, MN 55455 USA Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USAZhu, Xiao-Hong论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USA Univ Minnesota, Dept Radiol, Minneapolis, MN 55455 USA Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USAWhitley, Chester B.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Dept Pediat, Minneapolis, MN 55455 USA Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USAHackett, Perry B.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Dept Genet, Cell Biol Dev, Minneapolis, MN 55455 USA Univ Minnesota, Stem Cell Inst, Minneapolis, MN 55455 USA Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USALow, Walter C.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Biomed Engn Grad Program, Minneapolis, MN 55455 USA Univ Minnesota, Stem Cell Inst, Minneapolis, MN 55455 USA Univ Minnesota, Dept Neurosurg, Minneapolis, MN 55455 USA Univ Minnesota, Grad Program Neurosci, Minneapolis, MN 55455 USA Univ Minnesota, Ctr Magnet Resonance Res, Minneapolis, MN 55455 USA论文数: 引用数: h-index:机构:
- [22] Neonatal gene therapy of MPS I mice by intravenous injection of a lentiviral vectorMOLECULAR THERAPY, 2005, 11 (05) : 776 - 789Kobayashi, H论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Childrens Hosp Los Angeles, Keck Sch Med, Div Res Immunol BMT,Dept Pediat, Los Angeles, CA 90027 USACarbonaro, D论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Childrens Hosp Los Angeles, Keck Sch Med, Div Res Immunol BMT,Dept Pediat, Los Angeles, CA 90027 USAPepper, K论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Childrens Hosp Los Angeles, Keck Sch Med, Div Res Immunol BMT,Dept Pediat, Los Angeles, CA 90027 USAPetersen, D论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Childrens Hosp Los Angeles, Keck Sch Med, Div Res Immunol BMT,Dept Pediat, Los Angeles, CA 90027 USAGe, SD论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Childrens Hosp Los Angeles, Keck Sch Med, Div Res Immunol BMT,Dept Pediat, Los Angeles, CA 90027 USAJackson, H论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Childrens Hosp Los Angeles, Keck Sch Med, Div Res Immunol BMT,Dept Pediat, Los Angeles, CA 90027 USAShimada, H论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Childrens Hosp Los Angeles, Keck Sch Med, Div Res Immunol BMT,Dept Pediat, Los Angeles, CA 90027 USAMoats, R论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Childrens Hosp Los Angeles, Keck Sch Med, Div Res Immunol BMT,Dept Pediat, Los Angeles, CA 90027 USAKohn, DB论文数: 0 引用数: 0 h-index: 0机构: Univ So Calif, Childrens Hosp Los Angeles, Keck Sch Med, Div Res Immunol BMT,Dept Pediat, Los Angeles, CA 90027 USA
- [23] Gene therapy of MPS I mice using the Sleeping Beauty Transposon systemMOLECULAR GENETICS AND METABOLISM, 2009, 96 (02) : S26 - S26论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Bell, Jason论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minneapolis, MN USA Univ Minnesota, Minneapolis, MN USAKhan, Shaukat论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minneapolis, MN USA Univ Minnesota, Minneapolis, MN USAGunther, Roland论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minneapolis, MN USA Univ Minnesota, Minneapolis, MN USAParker, Josh论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minneapolis, MN USA Univ Minnesota, Minneapolis, MN USACarlson, Cathy论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minneapolis, MN USA Univ Minnesota, Minneapolis, MN USA论文数: 引用数: h-index:机构:Mclvor, R. Scott论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minneapolis, MN USA Univ Minnesota, Minneapolis, MN USAGupta, Pankaj论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Minneapolis, MN USA Univ Minnesota, Minneapolis, MN USA
- [24] Mapping brain networks in MPS I mice and their restoration following gene therapyScientific Reports, 13 (1)Wei Zhu论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance ResearchLi Ou论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance ResearchLin Zhang论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance ResearchIsaac H. Clark论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance ResearchYing Zhang论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance ResearchXiao-Hong Zhu论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance ResearchChester B. Whitley论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance ResearchPerry B. Hackett论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance ResearchWalter C. Low论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance ResearchWei Chen论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Center for Magnetic Resonance Research
- [25] Gene Therapy of Cancer:Induction of Anti-Tumor ImmunityCellular & Molecular Immunology, 2004, (02) : 105 - 111Jesus Prieto论文数: 0 引用数: 0 h-index: 0机构: Division of Hepatology and Gene Therapy
- [26] Gene Therapy of Cancer: Induction of Anti-Tumor ImmunityCELLULAR & MOLECULAR IMMUNOLOGY, 2004, 1 (02) : 105 - 111Qian, Cheng论文数: 0 引用数: 0 h-index: 0机构: Univ Navarra, Fdn Invest Med Aplicada, Sch Med, Div Hepatol & Gene Therapy, E-31080 Pamplona, Spain Univ Navarra, Fdn Invest Med Aplicada, Sch Med, Div Hepatol & Gene Therapy, E-31080 Pamplona, SpainPrieto, Jesus论文数: 0 引用数: 0 h-index: 0机构: Univ Navarra, Fdn Invest Med Aplicada, Sch Med, Div Hepatol & Gene Therapy, E-31080 Pamplona, Spain Univ Navarra, Fdn Invest Med Aplicada, Sch Med, Div Hepatol & Gene Therapy, E-31080 Pamplona, Spain
- [27] Neonatal retroviral vector-mediated gene therapy for MPS I in mice and catsMOLECULAR THERAPY, 2003, 7 (05) : S77 - S77Liu, YL论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, St Louis, MO USAXu, LF论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, St Louis, MO USAEllinwood, NM论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, St Louis, MO USAO'Malley, T论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, St Louis, MO USAHaskins, ME论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, St Louis, MO USAPonder, KP论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, St Louis, MO USA
- [28] Gene Therapy for MPS VI Is Effective in Cats without Pre-Existing Immunity to AAV8MOLECULAR THERAPY, 2013, 21 : S138 - S139Ferla, Rita论文数: 0 引用数: 0 h-index: 0机构: Telethon Inst Genet & Med TIGEM, Naples, Italy Univ Naples Federico II, Med Genet Dept Pediat, Naples, Italy Telethon Inst Genet & Med TIGEM, Naples, ItalyO'Malley, Thomas论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Telethon Inst Genet & Med TIGEM, Naples, ItalyCalcedo, Roberto论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA USA Telethon Inst Genet & Med TIGEM, Naples, ItalyO'Donnell, Patricia论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Telethon Inst Genet & Med TIGEM, Naples, ItalyWang, Ping论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Telethon Inst Genet & Med TIGEM, Naples, ItalyCotugno, Gabriella论文数: 0 引用数: 0 h-index: 0机构: Telethon Inst Genet & Med TIGEM, Naples, Italy Univ Naples Federico II, Med Genet Dept Pediat, Naples, Italy Telethon Inst Genet & Med TIGEM, Naples, ItalyClaudiani, Pamela论文数: 0 引用数: 0 h-index: 0机构: Telethon Inst Genet & Med TIGEM, Naples, Italy Univ Naples Federico II, Med Genet Dept Pediat, Naples, Italy Telethon Inst Genet & Med TIGEM, Naples, ItalyWilson, James M.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA USA Telethon Inst Genet & Med TIGEM, Naples, ItalyHaskins, Mark论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Telethon Inst Genet & Med TIGEM, Naples, ItalyAuricchio, Alberto论文数: 0 引用数: 0 h-index: 0机构: Telethon Inst Genet & Med TIGEM, Naples, Italy Univ Naples Federico II, Med Genet Dept Pediat, Naples, Italy Telethon Inst Genet & Med TIGEM, Naples, Italy
- [29] Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine modelMOLECULAR GENETICS AND METABOLISM, 2016, 119 (1-2) : 124 - 130Hinderer, Christian论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USABell, Peter论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USALouboutin, Jean-Pierre论文数: 0 引用数: 0 h-index: 0机构: Univ West Indies, Dept Basic Med Sci, Sect Anat, Kingston, Jamaica Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAKatz, Nathan论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAZhu, Yanqing论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USALin, Gloria论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAChoa, Ruth论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USABagel, Jessica论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAO'Donnell, Patricia论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAFitzgerald, Caitlin A.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USALangan, Therese论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAWang, Ping论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USACasal, Margret L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAHaskins, Mark E.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAWilson, James M.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA
- [30] Towards the gene therapy of LAD-I immunodeficient patientsHUMAN GENE THERAPY, 2017, 28 (12) : A20 - A21Almarza, E.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainMesa-Nunez, C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainDamian, C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainLeon-Rico, D.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainAldea, M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainCarrascoso, C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainLozano, M. L.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainGuenechea, G.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainThrasher, A. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Coll London ICH UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainBueren, J. A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain