Givosiran for acute intermittent porphyria

被引:0
|
作者
Baker, Holly
机构
来源
关键词
D O I
暂无
中图分类号
R57 [消化系及腹部疾病];
学科分类号
摘要
引用
收藏
页码:728 / 728
页数:1
相关论文
共 50 条
  • [21] German Real-World Experience of Patients with Diverse Features of Acute Intermittent Porphyria Treated with Givosiran
    Kubisch, Ilja
    Wohmann, Nils
    Wissniowski, Thaddaeus Till
    Stauch, Thomas
    Oettel, Lucienne
    Diehl-Wiesenecker, Eva
    Somasundaram, Rajan
    Stoelzel, Ulrich
    JOURNAL OF CLINICAL MEDICINE, 2024, 13 (22)
  • [22] Baseline urinary ALA and PBG as criteria for starting pharmacologic prophylactic treatment in acute intermittent porphyria treated with givosiran
    Kuo, Hung-Chou
    Ro, Long-Sun
    Lin, Chia-Ni
    Chu, Chu-che
    Liao, Ming-Feng
    Chang, Hong-Shiu
    MOLECULAR GENETICS AND METABOLISM REPORTS, 2024, 41
  • [23] Evaluating the Efficacy of a Small Interfering Ribonucleic Acid Molecule, Givosiran, in Treating Acute Intermittent Porphyria: A Systematic Review
    Patel, Priyansh
    Midha, Sidharth
    Shukla, Surmai
    Dhamija, Divyanshu
    Bello, Adedamola O.
    Khan, Safeera
    CUREUS JOURNAL OF MEDICAL SCIENCE, 2023, 15 (06)
  • [24] Acute intermittent porphyria
    Herrick, AL
    McColl, KEL
    BEST PRACTICE & RESEARCH CLINICAL GASTROENTEROLOGY, 2005, 19 (02) : 235 - 249
  • [25] ACUTE INTERMITTENT PORPHYRIA
    DAVIS, CA
    DAVIS, MG
    AMERICAN JOURNAL OF NURSING, 1960, 60 (06) : 847 - 850
  • [26] Acute intermittent porphyria
    Regan, L
    Gonsalves, L
    Tesar, G
    PSYCHOSOMATICS, 1999, 40 (06) : 521 - 523
  • [27] ACUTE INTERMITTENT PORPHYRIA
    DAY, RS
    EALES, L
    SOUTH AFRICAN MEDICAL JOURNAL, 1982, 61 (08): : 260 - 261
  • [28] ACUTE INTERMITTENT PORPHYRIA
    HORN, U
    ZENTRALBLATT FUR GYNAKOLOGIE, 1981, 103 (24): : 1556 - 1559
  • [29] Acute Intermittent Porphyria
    Scanameo, Alexandra
    Amin, Shefali
    Lee, Andrew E.
    Altomare, John F.
    AMERICAN JOURNAL OF GASTROENTEROLOGY, 2022, 117 (10): : S2100 - S2100
  • [30] INTERMITTENT ACUTE PORPHYRIA
    CLOTET, B
    PEREZ, C
    MARTINEZVAZQUEZ, JM
    MEDICINA CLINICA, 1979, 73 (01): : 32 - 38