Givosiran for acute intermittent porphyria

被引：0
|
作者：
Baker, Holly
机构：
来源：
LANCET GASTROENTEROLOGY & HEPATOLOGY | 2020年 / 5卷 / 08期
关键词：
D O I：
暂无
中图分类号：
R57 [消化系及腹部疾病];
学科分类号：
摘要：
引用
收藏
页码：728 / 728
页数：1
相关论文
共 50 条
  • [1] Givosiran for acute intermittent porphyria
    Baker, Holly
    LANCET GASTROENTEROLOGY & HEPATOLOGY, 2019, 4 (04): : 265 - 265
  • [2] Givosiran for Acute Intermittent Porphyria
    Goma-Garces, Elena
    Vanessa Perez-Gomez, M.
    Ortiz, Alberto
    NEW ENGLAND JOURNAL OF MEDICINE, 2020, 383 (20): : 1989 - 1989
  • [3] Acute intermittent porphyria, givosiran, and homocysteine
    Fontanellas, Antonio
    Avila, Matias A.
    Arranz, Elena
    Enriquez de Salamanca, Rafael
    Morales-Conejo, Montserrat
    JOURNAL OF INHERITED METABOLIC DISEASE, 2021, 44 (04) : 790 - 791
  • [4] Givosiran for the Treatment of Pediatric Acute Intermittent Porphyria
    Bujold, Kenneth E.
    Kasher, Nicole
    McKiernan, Christine
    JOURNAL OF PEDIATRIC HEMATOLOGY ONCOLOGY, 2024, 46 (07) : e524 - e527
  • [5] Personalized dosage of Givosiran in acute intermittent porphyria
    Montes, Manuel Garrido
    Mataix, Roberto Pertusa
    Morillo, Jose Salvador Garcia
    MEDICINA CLINICA, 2024, 163 (05): : 260 - 261
  • [6] Givosiran: a targeted treat ment for acute intermittent porphyria
    Dickey, Amy K.
    Leaf, Rebecca K.
    HEMATOLOGY-AMERICAN SOCIETY OF HEMATOLOGY EDUCATION PROGRAM, 2024, (01) : 426 - 433
  • [7] Givosiran in acute intermittent porphyria: A personalized medicine approach
    Poli, Antoine
    Schmitt, Caroline
    Moulouel, Boualem
    Mirmiran, Arienne
    Talbi, Neila
    Riviere, Sophie
    Cerutti, Diane
    Bouchoule, Isabelle
    Faivre, Anthony
    Grobost, Vincent
    Douillard, Claire
    Duchene, Francis
    Fiorentino, Valeria
    Dupre, Thierry
    Manceau, Hana
    Peoc'h, Katell
    Puy, Herve
    Lefebvre, Thibaud
    Gouya, Laurent
    MOLECULAR GENETICS AND METABOLISM, 2022, 135 (03) : 206 - 214
  • [8] Therapeutic developments in acute intermittent porphyria: The role of givosiran
    Poli, A.
    Schmitt, C.
    Moulouel, B.
    Mirmiran, A.
    Talbi, N.
    Riviere, S.
    Cerutti, D.
    Bouchoule, I.
    Faivre, A.
    Grobost, V.
    Douillard, C.
    Duchene, F.
    Fiorentino, V.
    Dupre, T.
    Manceau, H.
    Peoc'h, K.
    Puy, H.
    Lefebvre, T.
    Gouya, L.
    REVUE DE MEDECINE INTERNE, 2024, 45 : A30 - A32
  • [9] Acute intermittent porphyria: Acute flare-up resolved with givosiran
    Alonso, Ignacio Jara
    Lopez, Angel Manuel Ruedas
    Diaz, Ignacio Barbolla
    MEDICINA CLINICA, 2023, 161 (10): : 454 - 455
  • [10] Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria
    Balwani, Manisha
    Sardh, Eliane
    Ventura, Paolo
    Peiro, Paula Aguilera
    Rees, David C.
    Stoelzel, Ulrich
    Bissell, D. Montgomery
    Bonkovsky, Herbert L.
    Windyga, Jerzy
    Anderson, Karl E.
    Parker, Charles
    Silver, Samuel M.
    Keel, Sioban B.
    Wang, Jiaan-Der
    Stein, Penelope E.
    Harper, Pauline
    Vassiliou, Daphne
    Wang, Bruce
    Phillips, John
    Ivanova, Aneta
    Langendonk, Janneke G.
    Kauppinen, Raili
    Minder, Elisabeth
    Horie, Yutaka
    Penz, Craig
    Chen, Jihong
    Liu, Shangbin
    Ko, John J.
    Sweetser, Marianne T.
    Garg, Pushkal
    Vaishnaw, Akshay
    Kim, Jae B.
    Simon, Amy R.
    Gouya, Laurent
    NEW ENGLAND JOURNAL OF MEDICINE, 2020, 382 (24): : 2289 - 2301
12345