Dual-regulated lentiviral vector for gene therapy of x-linked chronic granulomatous disease

被引：0

作者：

Farinelli, G. ^{[1
]}

Hernandez, R. Jofra ^{[1
]}

Migliavacca, M. ^{[1
]}

Zonari, E. ^{[1
]}

Capo, V. ^{[1
]}

Chiriaco, M. ^{[2
,3
]}

Scaramuzza, S. ^{[1
]}

Di Matteo, G. ^{[2
,3
]}

Sergi, L. Sergi ^{[1
]}

Rossi, A. ^{[4
]}

Ranucci, S. ^{[4
]}

Bragonzi, A. ^{[4
]}

Kajaste-Rudnitski, A. ^{[1
]}

Trono, D. ^{[5
]}

Grez, M. ^{[6
]}

Rossi, P. ^{[2
,3
]}

Finocchi, A. ^{[2
,3
]}

Naldini, L. ^{[1
,7
]}

Gentner, B. ^{[1
]}

Aiuti, A. ^{[1
,7
]}

机构：

[1] Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

[2] Childrens Hosp Bambino Ges, Rome, Italy

[3] Tor Vergata Univ, Rome, Italy

[4] Ist Sci San Raffaele, Milan, Italy

[5] Ecole Polytech Fed Lausanne, CH-1015 Lausanne, Switzerland

[6] Georg Speyer Haus, Frankfurt, Germany

[7] Univ Vita Salute San Raffaele, Milan, Italy

来源：

HUMAN GENE THERAPY | 2015年 / 26卷 / 10期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P081

引用

页码：A51 / A51

页数：1

共 50 条

[21] A Gene Therapy Clinical Study of a Patient with X-Linked Chronic Granulomatous Disease
Kawai, Toshinao
Okamura, Kohji
Yagita, Mari
Goto, Fumihiro
Nakazawa, Yumiko
Uchiyama, Toru
Nakabayashi, Kazuhiko
Nunoi, Hiroyuki
Malech, Harry
Onodera, Masafumi
MOLECULAR THERAPY, 2016, 24 : S87 - S88
[22] X-linked chronic granulomatous disease
Roesler, Joachim
JOURNAL OF SMALL ANIMAL PRACTICE, 2006, 47 (09)
[23] Gene Therapy for X-Linked Chronic Granulomatous Disease (Net4CGD)
Galy, Anne
Thrasher, Adrian
Grez, Manuel
Schwaeble, Joachim
Reichenbach, Janine
Cavazzana, Marina
Pouillot, Severine
Kuehlcke, Klaus
Schmidt, Manfred
Paprotka, Tobias
Schreiber, Andreas
Koubi, David
HUMAN GENE THERAPY CLINICAL DEVELOPMENT, 2015, 26 (02) : 88 - 90
[24] Treatment of infections in patients with X-linked chronic granulomatous disease (CGD) with gene therapy
Kang, Elizabeth M.
Linton, Gilda
Theobald, Narda
O'Brien, Sandra Anaya
Hilligoss, Dianne
Malech, Harry L.
BLOOD CELLS MOLECULES AND DISEASES, 2008, 40 (02) : 270 - 271
[25] Treatment of infections in patients with X-linked Chronic Granulomatous Disease (XCGD) with gene therapy
Kang, Elizabeth M.
Linton, Gilda
Tbeobald, Narda
O'Brien, Sandra Anaya
Hilligoss, Dianne
Malech, Harry L.
BLOOD, 2007, 110 (11) : 155A - 155A
[26] Lentiviral gene therapy for X-linked agammaglobulinemia
Ng, Peter
Baert, Miranda R. M.
Pike-Overzet, Karin
Rodijk, Mark
Schambach, Axel
Baum, Christopher
van Til, Niek
Hendriks, Rudolf
Wagemaker, Gerard
van Dongen, Jacques
Staal, Frank J. T.
HUMAN GENE THERAPY, 2007, 18 (10) : 1011 - 1011
[27] Lentiviral Gene Therapy for X-linked Adrenoleukodystrophy
Cartier, Nathalie
HUMAN GENE THERAPY, 2010, 21 (04) : 490 - 490
[28] MSCV-h91Neo, a retroviral vector for gene therapy of X-linked chronic granulomatous disease.
Ding, C
Pech, N
Kume, A
Dinauer, MC
BLOOD, 1995, 86 (10) : 956 - 956
[29] Hematopoietic stem cell gene therapy with lentiviral vector in X-linked adrenoleukodystrophy
Cartier, N.
Hacein-Bey-Abina, S.
Bartholomae, C.
Schmidt, M.
Kutschera, I.
Vidaud, M.
Dal-Cortivo, L.
Malhaoui, N.
Bellesme, C.
Lefrere, F.
l'Homme, B.
Bougneres, P.
Fischer, A.
Von Kalle, C.
Cavazzana-Calvo, M.
Aubourg, P.
HUMAN GENE THERAPY, 2010, 21 (10) : 1367 - 1368
[30] Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
Cartier, Nathalie
Hacein-Bey-Abina, Salima
Bartholomae, Cynthia C.
Veres, Gabor
Schmidt, Manfred
Kutschera, Ina
Vidaud, Michel
Abel, Ulrich
Dal-Cortivo, Liliane
Caccavelli, Laure
Mahlaoui, Nizar
Kiermer, Veronique
Mittelstaedt, Denice
Bellesme, Celine
Lahlou, Najiba
Lefrere, Francois
Blanche, Stephane
Audit, Muriel
Payen, Emmanuel
Leboulch, Philippe
l'Homme, Bruno
Bougneres, Pierre
Von Kalle, Christof
Fischer, Alain
Cavazzana-Calvo, Marina
Aubourg, Patrick
SCIENCE, 2009, 326 (5954) : 818 - 823

← 1 2 3 4 5 →