Successful Induction of Immune Tolerance to Canine Factor VIII after Lentiviral-Mediated Gene Therapy in Neonatal Hemophilia A Mice

被引:0
|
作者
Matsui, Hideto [1 ]
Shibata, Masaru [1 ,2 ]
Brown, Brian [1 ]
Labelle, Andrea [1 ]
Hegadorn, Carol [1 ]
Andrews, Chandler [1 ]
Chuah, Marinee [3 ]
VandenDriessche, Thierry [3 ]
Miao, Carol H. [4 ]
Hough, Christine [1 ]
Lillicrap, David [1 ]
机构
[1] Queens Univ, Dept Pathol & Mol Med, Kingston, ON, Canada
[2] Nara Med Univ, Dept Pediat, Kashihara, Nara, Japan
[3] Univ Louvain, Flanders Interuniv Inst Biotechnol, Ctr Transgene Technol & Gene Therapy, Louvain, Belgium
[4] Univ Washington, Dept Pediat, Seattle, WA 98195 USA
关键词
D O I
10.1016/j.ymthe.2006.08.1193
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
1091
引用
收藏
页码:S419 / S419
页数:1
相关论文
共 50 条
  • [1] Intrathymic Induction of Factor VIII Specific Immune Tolerance in Hemophilia A Mice
    Peng, Baowei
    Lee, Lawrence
    Chen, Liping
    Jirovska, Dominika
    Miao, Carol
    MOLECULAR THERAPY, 2009, 17 : S247 - S247
  • [2] Long-term correction of hemophilia A mice following lentiviral mediated delivery of an optimized canine factor VIII gene
    J M Staber
    M J Pollpeter
    C-G Anderson
    M Burrascano
    A L Cooney
    P L Sinn
    D T Rutkowski
    W C Raschke
    P B McCray
    Gene Therapy, 2017, 24 : 742 - 748
  • [3] Long-term correction of hemophilia A mice following lentiviral mediated delivery of an optimized canine factor VIII gene
    Staber, J. M.
    Pollpeter, M. J.
    Anderson, C-G
    Burrascano, M.
    Cooney, A. L.
    Sinn, P. L.
    Rutkowski, D. T.
    Raschke, W. C.
    McCray, P. B.
    GENE THERAPY, 2017, 24 (11) : 742 - 748
  • [4] Induction of immune tolerance by neonatal intravenous injection of human factor VIII in murine hemophilia A
    Madoiwa, S
    Yamauchi, T
    Hakamata, Y
    Kobayashi, E
    Arai, M
    Sugo, T
    Mimuro, J
    Sakata, Y
    JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2004, 2 (05) : 754 - 762
  • [5] INDUCTION OF NEONATAL FC RECEPTOR-MEDIATED TOLERANCE TO THERAPEUTIC FACTOR VIII IN HEMOPHILIA A
    Reyes-Ruiz, A.
    Delignat, S.
    Mimoun, A.
    Daventure, V.
    Dimitrov, J. D.
    Lacroix-Desmazes, S.
    HAEMOPHILIA, 2022, 28 : 28 - 29
  • [6] Induction of neonatal Fc receptor-mediated tolerance to therapeutic factor VIII in Hemophilia A
    Reyes-Ruiz, Alejandra
    Delignat, Sandrine
    Daventure, Victoria
    Bhale, Aishwarya
    Venkataraman, Krishnan
    Dimitrov, Jordan D.
    Lacroix-Desmazes, Sebastien
    EUROPEAN JOURNAL OF IMMUNOLOGY, 2024, 54 : 1260 - 1260
  • [7] Enhancing Immune Regulation to Promote Tolerance to Factor VIII in Gene Therapy for Hemophilia A
    Butterfield, John S. S.
    Biswas, Moanaro
    Kumar, Sandeep R. P.
    Ling, Chen
    Terhorst, Cox
    Herzog, Roland W.
    MOLECULAR THERAPY, 2018, 26 (05) : 238 - 238
  • [8] Translational Potential of Immune Tolerance Induction by AAV Liver-Directed Factor VIII Gene Therapy for Hemophilia A
    Samelson-Jones, Benjamin J.
    Arruda, Valder R.
    FRONTIERS IN IMMUNOLOGY, 2020, 11
  • [10] Ultrasound and Microbubbles Mediated Factor VIII Plasmid Gene Therapy in Hemophilia A Mice
    Song, Shuxian
    Noble, Misty L.
    Sun, Ryan
    Fan, Luping
    Miao, Carol H.
    MOLECULAR THERAPY, 2013, 21 : S41 - S42