[1] Ist Sci San Raffaele, IRCCS, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy
[2] Univ Vita Salute San Raffaele, Milan, Italy
[3] Ist Sci San Raffaele, IRCCS, Pediat Immunohematol & Bone Marrow Transplantat U, Milan, Italy
[4] Ist Sci San Raffaele, IRCCS, Hematol & Bone Marrow Transplantat Unit, Milan, Italy
[5] Fdn Telethon, Milan, Italy