The EHA Research Roadmap: Hematopoietic Stem Cell Gene Therapy

被引:6
|
作者
Naldini, Luigi [1 ,2 ]
Cicalese, Maria Pia [1 ,3 ]
Bernardo, Maria Ester [1 ,2 ,3 ]
Gentner, Bernhard [1 ,4 ]
Gabaldo, Michela [1 ,5 ]
Ferrari, Giuliana [1 ,2 ]
Aiuti, Alessandro [1 ]
机构
[1] Ist Sci San Raffaele, IRCCS, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy
[2] Univ Vita Salute San Raffaele, Milan, Italy
[3] Ist Sci San Raffaele, IRCCS, Pediat Immunohematol & Bone Marrow Transplantat U, Milan, Italy
[4] Ist Sci San Raffaele, IRCCS, Hematol & Bone Marrow Transplantat Unit, Milan, Italy
[5] Fdn Telethon, Milan, Italy
来源
HEMASPHERE | 2022年 / 6卷 / 02期
关键词
D O I
10.1097/HS9.0000000000000671
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
In 2016, the European Hematology Association (EHA) published the EHA Roadmap for European Hematology Research1 aiming to highlight achievements in the diagnostics and treatment of blood disorders, and to better inform European policy makers and other stakeholders about the urgent clinical and scientific needs and priorities in the field of hematology. Each section was coordinated by 1 to 2 section editors who were leading international experts in the field. In the 5 years that have followed, advances in the field of hematology have been plentiful. As such, EHA is pleased to present an updated Research Roadmap, now including 11 sections, each of which will be published separately. The updated EHA Research Roadmap identifies the most urgent priorities in hematology research and clinical science, therefore supporting a more informed, focused, and ideally a more funded future for European hematology research. The 11 EHA Research Roadmap sections include Normal Hematopoiesis; Malignant Lymphoid Diseases; Malignant Myeloid Diseases; Anemias and Related Diseases; Platelet Disorders; Blood Coagulation and Hemostatic Disorders; Transfusion Medicine; Infections in Hematology; Hematopoietic Stem Cell Transplantation; CAR-T and Other Cellbased Immune Therapies; and Gene Therapy. Copyright © 2022 the Author(s).
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页数:10
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