共 50 条
- [12] Pharmacological chaperone therapy for Fabry disease [J]. PROCEEDINGS OF THE JAPAN ACADEMY SERIES B-PHYSICAL AND BIOLOGICAL SCIENCES, 2012, 88 (01): : 18 - 30
- [13] Gene therapy for Fabry disease. [J]. AMERICAN JOURNAL OF HUMAN GENETICS, 2001, 69 (04) : 678 - 678
- [16] Enzyme replacement therapy and Fabry kidney disease [J]. CLINICAL THERAPEUTICS, 2007, 29 : S96 - S98
- [18] Gene Therapy for Fabry Disease: A Review of the Literature [J]. BIODRUGS, 2013, 27 (03) : 237 - 246