Epigenome editing of MECP2 rescues Rett syndrome neurons

被引:1
|
作者
Lempriere, Sarah
机构
[1] Nature Reviews Neurology,
关键词
D O I
10.1038/s41582-023-00778-2
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
In a new study, targeted editing of the epigenome was found to reactivate silenced MECP2 in human embryonic stem cells, suggesting that a similar approach could be used to treat Rett syndrome in girls.
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收藏
页码:127 / 127
页数:1
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