Nonhuman primate model of Usher Syndrome Type 1B: course of retinal degeneration and initial gene therapy results

被引:0
|
作者
Renner, Lauren [1 ]
Ryu, Junghyun [2 ]
Hennebold, Jon D. [2 ]
Boye, Sanford L. [3 ]
Hanna, Carol [2 ]
Burch, Fernanda [2 ]
Kempton, Beth [4 ]
Porsov, Edward V. [4 ]
Spears, Rachel [1 ]
Burwitz, Benjamin [5 ]
Lauer, Andreas K. [6 ]
Wilson, David [6 ]
Pennesi, Mark E. [6 ]
Boye, Shannon [7 ]
Brigande, John V. [4 ]
Neuringer, Martha [1 ,6 ]
机构
[1] Oregon Hlth & Sci Univ, Oregon Natl Primate Res Ctr, Neurosci, Beaverton, OR USA
[2] Oregon Hlth & Sci Univ, Reprod & Dev Sci, Oregon Natl Primate Res Ctr, Beaverton, OR USA
[3] Univ Florida, Powell Gene Therapy Ctr, Pediat, Gainesville, FL USA
[4] Oregon Hlth & Sci Univ, Otolaryngol, Portland, OR USA
[5] Oregon Hlth & Sci Univ, Vaccine & Gene Therapy Inst, Portland, OR USA
[6] Oregon Hlth & Sci Univ, Casey Eye Inst, Portland, OR USA
[7] Univ Florida, Div Cellular & Mol Therapy, Pediat, Gainesville, FL USA
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中图分类号
R77 [眼科学];
学科分类号
100212 ;
摘要
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页数:4
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