Lentiviral vectors as gene therapy vehicles of Usher syndrome 1B

被引:0
|
作者
Yang, XJ
Hashimoto, T
Zhang, XM
Azarian, SM
Lillo, C
Gibbs, D
Williams, DS
机构
关键词
D O I
暂无
中图分类号
R77 [眼科学];
学科分类号
100212 ;
摘要
5223
引用
收藏
页数:1
相关论文
共 50 条
  • [1] Lentiviral gene replacement therapy of retinas in a mouse model for Usher syndrome type 1B
    T Hashimoto
    D Gibbs
    C Lillo
    S M Azarian
    E Legacki
    X-M Zhang
    X-J Yang
    D S Williams
    [J]. Gene Therapy, 2007, 14 : 584 - 594
  • [2] Lentiviral gene replacement therapy of retinas in a mouse model for Usher syndrome type 1B
    Hashimoto, T.
    Gibbs, D.
    Lillo, C.
    Azarian, S. M.
    Legacki, E.
    Zhang, X-M
    Yang, X-J
    Williams, D. S.
    [J]. GENE THERAPY, 2007, 14 (07) : 584 - 594
  • [3] Gene Therapy Strategies for Usher Syndrome Type 1B
    Williams, David S.
    Lopes, Vanda S.
    [J]. RETINAL DEGENERATIVE DISEASES, 2012, 723 : 235 - 242
  • [4] Third-generation lentiviral gene therapy rescues function in a mouse model of Usher 1B
    Schott, Juliane W.
    Huang, Peixin
    Morgan, Michael
    Nelson-Brantley, Jennifer
    Koehler, Ally
    Renslo, Bryan
    Buening, Hildegard
    Warnecke, Athanasia
    Schambach, Axel
    Staecker, Hinrich
    [J]. MOLECULAR THERAPY, 2023, 31 (12) : 3502 - 3519
  • [5] Models for Usher syndrome 1B
    Lillo, C
    Kitamoto, J
    Liu, XR
    Quint, E
    Steel, KP
    Williams, DS
    [J]. RETINAL DEGENERATIONS: MECHANISMS AND EXPERIMENTAL THERAPY, 2003, 533 : 143 - 150
  • [6] Lentiviral Gene Therapies for Wet AMD, Stargardt Macula Dystrophy and Usher Syndrome 1B: Clinical Trial Updates
    Lad, Yatish
    Mitrophanous, Kyriacos
    Ellis, Scott
    Adams, Nicola
    Binley, Katie
    Kelleher, Michelle
    Lucas, Cherry
    Davies, Madhu
    [J]. MOLECULAR THERAPY, 2014, 22 : S50 - S50
  • [7] Lentiviral Gene therapies for wet AMD, Stargardt macula dystrophy and Usher Syndrome 1B: clinical trial updates
    Davies, Madhu
    Ellis, Scott
    Adams, Nicola
    Binley, Katie
    Kelleher, Michelle
    Mitrophanous, Kyriacos
    [J]. INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2014, 55 (13)
  • [8] Screen for Usher syndrome 1B mutations in the ovine myosin viia gene
    Slatter, T
    Azarian, SM
    Tebbutt, S
    Maw, M
    Williams, DS
    [J]. RETINAL DEGENERATIONS: MECHANISMS AND EXPERIMENTAL THERAPY, 2003, 533 : 151 - 155
  • [9] DEFECTIVE MYOSIN VIIA GENE RESPONSIBLE FOR USHER SYNDROME TYPE 1B
    WELL, D
    BLANCHARD, S
    KAPLAN, J
    GUILFORD, P
    GIBSON, F
    WALSH, J
    MBURU, P
    VARELA, A
    LEVILLERS, J
    WESTON, MD
    KELLEY, PM
    KIMBERLING, WJ
    WAGENAAR, M
    LEVIACOBAS, F
    LARGETPIET, D
    MUNNICH, A
    STEEL, KP
    BROWN, SDM
    PETIT, C
    [J]. NATURE, 1995, 374 (6517) : 60 - 61
  • [10] Evaluation of visual impairment in Usher syndrome 1b and Usher syndrome 2a
    Pennings, RJE
    Huygen, PLM
    Orten, DJ
    Wagenaar, M
    van Aarem, A
    Kremer, H
    Kimberling, WJ
    Cremers, CWRJ
    Deutman, AF
    [J]. ACTA OPHTHALMOLOGICA SCANDINAVICA, 2004, 82 (02): : 131 - 139