Development of Rationally Designed CAG-Based Promoters for Use in Gene Therapy

被引:0
|
作者
Lee, Dustin [1 ]
Sullivan, Josefa M. [1 ]
Fabela, Natalia [1 ]
Hernandez, Edgar [1 ]
During, Matthew J. [1 ]
Forbes, Alexandria [1 ]
Liu, Ce Feng [1 ]
机构
[1] MeiraGTx LLC, Mol & Prot Engn, New York, NY USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
1277
引用
收藏
页码:606 / 607
页数:2
相关论文
共 50 条
  • [31] Use of nonviral promoters in adenovirus-mediated gene therapy: reduction of lysosomal storage in the aspartylglucosaminuria mouse
    Virta, Salli
    Rapola, Juhani
    Jalanko, Anu
    Laine, Minna
    JOURNAL OF GENE MEDICINE, 2006, 8 (06): : 699 - 706
  • [32] Novel, high expressing and antibiotic-controlled plasmid vectors designed for use in gene therapy
    Liang, X
    Hartikka, J
    Sukhu, L
    Manthorpe, M
    Hobart, P
    GENE THERAPY, 1996, 3 (04) : 350 - 356
  • [33] Elucidation of promoters for disease-regulated gene and cell-based therapy for rheumatoid arthritis
    Geurts, Jeroen
    Arntz, Onno
    Van Raaij, Annemiek
    Bennink, Miranda
    Veenbergen, Sharon
    Joosten, Leo
    Van den Berg, Wim
    van de Loo, Fons
    HUMAN GENE THERAPY, 2007, 18 (10) : 1077 - 1077
  • [34] Evaluating Tissue Specific Promoters Using Adeno-Associated Virus Based Gene Therapy
    Zielinska, Nicole
    Pei, Yanlong
    Howard, Erin L.
    Stevens, Brenna A. Y.
    Goens, Melanie M.
    Campbell, Elena S. B.
    Hughes, Madison E.
    Zheng, Dinghai
    Gordon, Benjamin
    Nielsen, Alec
    Caswell, Jeff
    Arroyo, Luis G.
    Srinivas, Raja R.
    Wootton, Sarah K.
    MOLECULAR THERAPY, 2024, 32 (04) : 695 - 696
  • [35] Analysis of promoters and expression-targeted gene therapy optimization based on doubling time and transfectability
    Dobek, Georgina L.
    Zhang, Xiujuan
    Balazs, Daniel A.
    Godbey, W. T.
    FASEB JOURNAL, 2011, 25 (09): : 3219 - 3228
  • [36] Process Development in Single use to Facilitate cGMP in Gene Therapy
    Carrondo, Manuel
    HUMAN GENE THERAPY, 2012, 23 (10) : A21 - A21
  • [37] High affinity antibody based on a rationally designed hapten and development of a chemiluminescence enzyme immunoassay for quantification of Alternariol in fruit Juice, maize and flour
    Yao, Chan-Yuan
    Xu, Zhen-Lin
    Wang, Hong
    Zhu, Fan
    Luo, Lin
    Yang, Jin-Yi
    Sun, Yuan-Ming
    Lei, Hong-Tao
    Tian, Yuan-Xin
    Shen, Yu-Dong
    FOOD CHEMISTRY, 2019, 283 : 359 - 366
  • [38] Gene therapy for prostate cancer; Development of tissue specific promoter-based gene therapy
    Gotoh, A
    Shirakawa, T
    Wada, Y
    Ko, SC
    Kao, CH
    Chung, LWK
    Kamidono, S
    FRONTIERS IN HUMAN GENETICS: DISEASES AND TECHNOLOGIES, 2001, : 363 - 376
  • [39] Process development for the manufacture of plasmid DNA vectors for use in gene therapy
    Marquet, M
    Horn, NA
    Meek, JA
    BIOPHARM-THE TECHNOLOGY & BUSINESS OF BIOPHARMACEUTICALS, 1995, 8 (07): : 26 - &
  • [40] A first-in-human phase 1 clinical gene therapy trial for the treatment of heart failure using a novel rationally designed cardiotropic adeno-associated vector
    Alvisi, Monica
    Henry, Timothy
    Chung, Eugene
    Traverse, Jay
    Ervin, Leigh
    Krupa, Shiva
    Sadek, Hesham
    Jiang, Canwen
    Mikhail, Sheila
    Haghighi, Kobra
    Kranias, Evangelia
    Samulski, Jude
    Tretalova, Anna
    Hajjar, Roger
    JOURNAL OF MOLECULAR AND CELLULAR CARDIOLOGY, 2022, 173 : S113 - S113