Precise Correction of Duchenne Muscular Dystrophy with Exon 51 Deletion by Adenine Base Editing-Induced Exon Skipping in a Humanized Mouse Model

被引：0
|
作者：
Li, Guoling [1 ]
Lin, Jiajia [2 ]
Jin, Ming [2 ]
Li, Zhifang [3 ]
Xiao, Qingquan [1 ]
Shi, Linyu [1 ]
Wang, Ning [2 ]
Chen, Wanjin [2 ]
Xu, Chunlong [3 ]
Yang, Hui [1 ,4 ]
机构：
[1] HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China
[2] Fujian Med Univ, Affiliated Hosp 1, Dept Neurol, Fuzhou, Peoples R China
[3] Lingang Lab, Shanghai, Peoples R China
[4] Chinese Acad Sci, Ctr Excellence Brain Sci & Intelligence Technol, Shanghai, Peoples R China
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
667
引用
收藏
页码：333 / 334
页数：2
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