Precise Correction of Duchenne Muscular Dystrophy with Exon 51 Deletion by Adenine Base Editing-Induced Exon Skipping in a Humanized Mouse Model

被引：0

作者：

Li, Guoling ^{[1
]}

Lin, Jiajia ^{[2
]}

Jin, Ming ^{[2
]}

Li, Zhifang ^{[3
]}

Xiao, Qingquan ^{[1
]}

Shi, Linyu ^{[1
]}

Wang, Ning ^{[2
]}

Chen, Wanjin ^{[2
]}

Xu, Chunlong ^{[3
]}

Yang, Hui ^{[1
,4
]}

机构：

[1] HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China

[2] Fujian Med Univ, Affiliated Hosp 1, Dept Neurol, Fuzhou, Peoples R China

[3] Lingang Lab, Shanghai, Peoples R China

[4] Chinese Acad Sci, Ctr Excellence Brain Sci & Intelligence Technol, Shanghai, Peoples R China

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

667

引用

页码：333 / 334

页数：2

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