Liver-directed AAV gene therapy corrects disease symptoms in a murine model of lysosomal acid lipase deficiency

被引：0
|
作者：
Lam, Patricia [1 ]
Zygmunt, Deborah [1 ]
Ashbrook, Anna [1 ]
Yan, Cong [2 ]
Du, Hong [2 ]
Martin, Paul T. [1 ]
机构：
[1] Nationwide Childrens Hosp, Abigail Wexner Res Inst, Columbus, OH USA
[2] Indiana Univ Sch Med, Indianapolis, IN USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2023.107930
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
191
引用
收藏
页数：1
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