Liver-Directed Gene Therapy for Ornithine Aminotransferase Deficiency

被引：0

作者：

Boffa, Iolanda ^{[1
]}

Polishchuk, Elena ^{[1
]}

De Stefano, Lucia ^{[1
]}

Dell' Aquila, Fabio ^{[1
]}

Nusco, Edoardo ^{[1
]}

Marrocco, Elena ^{[1
]}

Audano, Matteo ^{[2
]}

Silvia, Pedretti ^{[2
]}

Caterino, Marianna ^{[3
,4
]}

Bellezza, Ilaria ^{[5
]}

Ruoppolo, Margherita ^{[3
,4
]}

Mitro, Nico ^{[2
,6
]}

Cellini, Barbara ^{[5
]}

Auricchio, Alberto ^{[1
,7
]}

Brunetti-Pierri, Nicola ^{[1
,8
,9
]}

机构：

[1] Telethon Inst Genet & Med TIGEM, Naples, Italy

[2] Univ Milan, Dept Pharmacol & Biomol Sci, Milan, Italy

[3] Univ Naples Federico II, Dept Mol Med & Med Biotechnol, Naples, Italy

[4] CEINGE Biotecnol Avanzate Scrl, Naples, Italy

[5] Univ Perugia, Sect Physiol & Biochem, Dept Expt Med, Perugia, Italy

[6] European Inst Oncol IRCCS, Dept Expt Oncol, IEO, Milan, Italy

[7] Univ Naples Federico II, Dept Adv Biomed Sci, Naples, Italy

[8] Univ Naples Federico II, Dept Translat Med, Naples, Italy

[9] Univ Naples Federico II, Sch Adv Studies, Genom & Expt Med Program, Scuola Super Meridionale SSM, Naples, Italy

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

642

引用

页码：322 / 322

页数：1

共 50 条

[1] Liver-directed gene therapy for ornithine aminotransferase deficiency
Boffa, Iolanda
Polishchuk, Elena
De Stefano, Lucia
Dell'Aquila, Fabio
Nusco, Edoardo
Marrocco, Elena
Audano, Matteo
Pedretti, Silvia
Caterino, Marianna
Bellezza, Ilaria
Ruoppolo, Margherita
Mitro, Nico
Cellini, Barbara
Auricchio, Alberto
Brunetti-Pierri, Nicola
[J]. EMBO MOLECULAR MEDICINE, 2023, 15 (04)
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[J]. MEDICAL CLINICS OF NORTH AMERICA, 1996, 80 (05) : 1201 - &
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