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- [21] STUDY DESIGN AND RATIONALE OF HELIOS-B: A PHASE 3 STUDY TO EVALUATE THE CLINICAL EFFICACY AND SAFETY OF VUTRISIRAN IN PATIENTS WITH ATTR AMYLOIDOSIS WITH CARDIOMYOPATHYJOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, 2020, 75 (11) : 3579 - 3579Shilling, Rebecca论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USAKarsten, Verena论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USASilliman, Nancy论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USAChen, Jihong论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USALi, Wei论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USAVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Alnylam Pharmaceut, Cambridge, MA USA
- [22] Impact of prior TTR stabilizer use in patients with hereditary Transthyretin-Mediated Amyloidosis in the APOLLO phase-3 study of PatisiranEUROPEAN JOURNAL OF NEUROLOGY, 2018, 25 : 17 - 18Coelho, T.论文数: 0 引用数: 0 h-index: 0机构: CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceAdams, D.论文数: 0 引用数: 0 h-index: 0机构: CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, France CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceGonzalez-Duarte, A.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Med Sci & Nutr Salvador Zubiran INCMNSZ, Mexico City, DF, Mexico CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceO'Riordan, W.论文数: 0 引用数: 0 h-index: 0机构: EStudy Site, Lamesa, CA USA CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceYang, C-C.论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ Hosp, Taipei, Taiwan CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceYamashita, T.论文数: 0 引用数: 0 h-index: 0机构: Kumamoto Univ Hosp, Kumamoto, Japan CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceKristen, A.论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Heidelberg, Germany CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceTournev, I.论文数: 0 引用数: 0 h-index: 0机构: New Bulgarian Univ, Sofia Med Univ, Univ Hosp Alexandrovska, Dept Neurol,Dept Cognit Sci & Psychol, Sofia, Bulgaria CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceSchmidt, H.论文数: 0 引用数: 0 h-index: 0机构: Univ Klinikum Munster, Munster, Germany CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, France论文数: 引用数: h-index:机构:Lin, K-P.论文数: 0 引用数: 0 h-index: 0机构: Taipei Vet Gen Hosp, Taipei, Taiwan CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceGandhi, P.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceSweetser, M.论文数: 0 引用数: 0 h-index: 0机构: Biogen Idec Inc, Cambridge, MA USA CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceChen, J.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceGoyal, S.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceGollob, J.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, FranceSuhr, O.论文数: 0 引用数: 0 h-index: 0机构: CHU Bicetre, Neurol Adulte NNERF French Reference Ctr FAP & Ot, Le Kremlin Bicetre, France
- [23] Impact of patisiran on norfolk QOL-DN in patients with hereditary transthyretin-mediated amyloidosis: results from the cardiac subpopulation in the phase 3 apollo studyEUROPEAN JOURNAL OF HEART FAILURE, 2018, 20 : 383 - 383Merlini, G.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Policolin San Matteo, Pavia, Italy IRCCS Policolin San Matteo, Pavia, ItalySolomon, S.论文数: 0 引用数: 0 h-index: 0机构: Brigham & Womens, Boston, MA USA IRCCS Policolin San Matteo, Pavia, ItalyAdams, D.论文数: 0 引用数: 0 h-index: 0机构: CHU Bicetre, INSERM, U1195, Natl Reference Ctr FAP NNERF,APHP, Le Kremlin Bicetre, France IRCCS Policolin San Matteo, Pavia, ItalyCoelho, T.论文数: 0 引用数: 0 h-index: 0机构: Hosptial Santo Antonio, Porto, Portugal IRCCS Policolin San Matteo, Pavia, ItalyDamy, T.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Est Creteil Val De Marne, Paris, France IRCCS Policolin San Matteo, Pavia, ItalyMauer, M.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, New York Presbyterian Hosp, HCM Ctr, Med Ctr, New York, NY USA IRCCS Policolin San Matteo, Pavia, ItalyPartisano, A. M.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA IRCCS Policolin San Matteo, Pavia, ItalyChen, J.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA IRCCS Policolin San Matteo, Pavia, ItalyKarsten, V.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA IRCCS Policolin San Matteo, Pavia, ItalyVest, J.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA IRCCS Policolin San Matteo, Pavia, ItalySuhr, O. L. E.论文数: 0 引用数: 0 h-index: 0机构: Umea Univ Hosp, Umea, Sweden IRCCS Policolin San Matteo, Pavia, ItalyKristen, A.论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Heidelberg, Germany IRCCS Policolin San Matteo, Pavia, Italy
- [24] Changes in neuropathy stage in patients with hATTR amyloidosis following patisiran treatment: Analysis from APOLLOJOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2018, 23 (04) : 400 - 400Gonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoAdams, David论文数: 0 引用数: 0 h-index: 0机构: CHU Bicetre, INSERM U1195, Natl Reference Ctr FAP NNERF, AP HP, Le Kremlin Bicetre, France Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoO'Riordan, William论文数: 0 引用数: 0 h-index: 0机构: eStudy Site, La Mesa, CA USA Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoYang, Chih-Chao论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ Hosp, Taipei, Taiwan Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoYamashita, Taro论文数: 0 引用数: 0 h-index: 0机构: Kumamoto Univ Hosp, Kumamoto, Japan Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoKristen, Arnt论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Heidelberg, Germany Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoTournev, Ivaylo论文数: 0 引用数: 0 h-index: 0机构: Univ Multiprofile Hosp Act Treatment, Sofia, Bulgaria Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoSchmidt, Hartmut论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Muenster, Munster, Germany Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Hosp Santo Antonio, Porto, Portugal Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico论文数: 引用数: h-index:机构:Ghandi, Pritesh论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoChen, Jihong论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoGollob, Jared论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoGoyal, Sunita论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoSuhr, Ole论文数: 0 引用数: 0 h-index: 0机构: Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico
- [25] Quality of life outcomes in APOLLO, the phase 3 trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosisAMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2020, 27 (03): : 153 - 162Obici, Laura论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, Italy Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Med Ctr, Amyloidosis Ctr, Boston, MA USA Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Porto, Hosp Santo Antonio, Porto, Portugal Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyGillmore, Julian论文数: 0 引用数: 0 h-index: 0机构: UCL, Natl Amyloidosis Ctr, Div Med, London, England Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalySchmidt, Hartmut H. -J.论文数: 0 引用数: 0 h-index: 0机构: Univ Munster, Med Clin Gastroenterol & Hepatol, Munster, Germany Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalySchilling, Matthias论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Munster, Inst Translat Neurol, Dept Neurol, Munster, Germany Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyYamashita, Taro论文数: 0 引用数: 0 h-index: 0机构: Kumamoto Univ, Dept Neurol, Kumamoto, Japan Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyLabeyrie, Celine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Sud, Ctr Hosp Univ Bicetre, AP HP,INSERM Unite, French Natl Reference Ctr Familial Amyloidot Poly, Paris, France Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyBrannagan, Thomas H., III论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyAjroud-Driss, Senda论文数: 0 引用数: 0 h-index: 0机构: Northwestern Univ, Feinberg Sch Med, Dept Neurol, Chicago, IL 60611 USA Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyGorevic, Peter论文数: 0 引用数: 0 h-index: 0机构: Mt Sinai Med Ctr, Dept Med, New York, NY 10029 USA Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyKristen, Arnt V.论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Dept Cardiol, Heidelberg, Germany Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyFranklin, Jaclyn论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Voyager Therapeut, 75 Sidney St, Cambridge, MA USA Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyChen, Jihong论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalySweetser, Marianne T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyWang, Jing Jing论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, ItalyAdams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Sud, Ctr Hosp Univ Bicetre, AP HP,INSERM Unite, French Natl Reference Ctr Familial Amyloidot Poly, Paris, France Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Viale Golgi 19, I-27100 Pavia, Italy
- [26] Patisiran, an RNAi therapeutic for patients with hereditary transthyretin-mediated amyloidosis: Sub-analysis in Japanese patients from the APOLLO studyNEUROLOGY AND CLINICAL NEUROSCIENCE, 2020, 8 (05): : 251 - 260Yamashita, Taro论文数: 0 引用数: 0 h-index: 0机构: Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, Japan Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, JapanUeda, Mitsuharu论文数: 0 引用数: 0 h-index: 0机构: Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, Japan Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, JapanKoike, Haruki论文数: 0 引用数: 0 h-index: 0机构: Nagoya Univ, Dept Neurol, Grad Sch Med, Nagoya, Aichi, Japan Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, JapanSekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ, Sch Med, Dept Med Neurol & Rheumatol, Matsumoto, Nagano, Japan Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, Japan论文数: 引用数: h-index:机构:Kodaira, Minori论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ, Sch Med, Dept Med Neurol & Rheumatol, Matsumoto, Nagano, Japan Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, Japan论文数: 引用数: h-index:机构:Sobue, Gen论文数: 0 引用数: 0 h-index: 0机构: Nagoya Univ, Dept Neurol, Grad Sch Med, Nagoya, Aichi, Japan Nagoya Univ, Brain & Mind Res Ctr, Grad Sch Med, Nagoya, Aichi, Japan Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, JapanZhang, Xiaoping论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut Inc, Cambridge, MA USA Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, JapanWhite, Matthew T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut Inc, Cambridge, MA USA Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, JapanSweetser, Marianne T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut Inc, Cambridge, MA USA Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, JapanWang, Jing Jing论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut Inc, Cambridge, MA USA Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, JapanAndo, Yukio论文数: 0 引用数: 0 h-index: 0机构: Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, Japan Nagasaki Int Univ, Dept Amyloidosis Pathol, Nagasaki, Japan Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, Japan
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