Partial orphan cancer drugs: FDA approval, clinical benefit, trials, epidemiology, price, beneficiaries, and spending

被引:0
|
作者
Michaeli, D. T. [1 ]
Michaeli, C. T. [2 ]
机构
[1] Heidelberg Univ Hosp, Natl Ctr Tumor Dis, Dept Med Oncol, Heidelberg, Germany
[2] UMM Univ Klinikum Mannheim, Abteilung Personalisierte Onkol Schwerpunkt Lung, Mannheim, Germany
关键词
D O I
10.1016/j.annonc.2023.09.2650
中图分类号
R73 [肿瘤学];
学科分类号
100214 ;
摘要
1696MO
引用
收藏
页码:S927 / S927
页数:1
相关论文
共 50 条
  • [21] Participation of African Americans in Clinical Trials Supporting FDA Approval of Hematological Malignancies Drugs
    Al Hadidi, Samer
    Miller-Chism, Courtney
    Mims, Martha
    Kamble, Rammurti
    CLINICAL LYMPHOMA MYELOMA & LEUKEMIA, 2019, 19 : S212 - S212
  • [22] Characteristics of clinical trials to support approval of orphan drugs for neurological disorders by the Japanese regulatory agency
    Nakamura, H.
    Takeda, S.
    Iwasaki, M.
    JOURNAL OF THE NEUROLOGICAL SCIENCES, 2017, 381 : 847 - 847
  • [23] Clinical Benefit and Regulatory Outcomes of Cancer Drugs Receiving Accelerated Approval
    Liu, Ian T. T.
    Kesselheim, Aaron S.
    Cliff, Edward R. Scheffer
    JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 2024, 331 (17): : 1471 - 1479
  • [24] Clinical Benefit, Price, and Regulatory Approval of Cancer Drugs Granted Breakthrough Therapy Designation in China, 2020-2024
    Luo, Xingxian
    Du, Xin
    Lv, Xufeng
    Yang, Yue
    Zhang, Xiaohong
    Huang, Lin
    JAMA NETWORK OPEN, 2024, 7 (10)
  • [25] Gender-based disparities in clinical trials supporting FDA approval of oncology drugs.
    Zettler, Marjorie
    Feinberg, Bruce A.
    Kish, Jonathan
    Gajra, Ajeet
    JOURNAL OF CLINICAL ONCOLOGY, 2020, 38 (15)
  • [26] New cancer drugs: paying a high price for clinical benefit?
    Pinn, Stephen
    BRITISH JOURNAL OF HOSPITAL MEDICINE, 2011, 72 (01) : 10 - 10
  • [27] Representation of women in clinical trials supporting FDA-approval of contemporary cancer therapies
    Kalathoor, Sujay
    Ghazi, Sanam
    Otieno, Beryl
    Babcook, Melissa A.
    Chen, Sunnia
    Nidhi, Neha
    Bae, Junu
    Pierre-Charles, Jovan
    Breathett, Khadijah
    Mazimba, Sula
    Johnson, Amber
    Brewer, LaPrincess
    Mohammed, Selma
    Carter, Rebecca R.
    Bonsu, Janice M.
    Ferdousi, Mussammat
    Kola-Kehinde, Onaopepo
    McLaughlin, Eric
    Brammer, Jonathan
    Ruz, Patrick
    Khan, Sarah
    Odei, Bismarck
    Mitchell, Darrion
    Wei, Lai
    Patel, Prem
    Paskett, Electra D.
    Addison, Daniel
    INTERNATIONAL JOURNAL OF CANCER, 2024, 155 (11) : 1958 - 1968
  • [28] Reporting of Cardiovascular Events in Clinical Trials Supporting FDA Approval of Contemporary Cancer Therapies
    Bonsu, Janice M.
    Guha, Avirup
    Charles, Lawrence
    Yildiz, Vedat O.
    Wei, Lai
    Baker, Brandee
    Brammer, Jonathan E.
    Awan, Farrukh
    Lustberg, Maryam
    Reinbolt, Raquel
    Miller, Eric D.
    Jneid, Hani
    Ruz, Patrick
    Carter, Rebecca R.
    Milks, Michael W.
    Paskett, Electra D.
    Addison, Daniel
    JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, 2020, 75 (06) : 620 - 628
  • [29] Systematic review of a personalized strategy in cancer clinical trials leading to FDA approval.
    Jardim, Denis Leonardo Fontes
    Schwaederle, Maria Clemence
    Lee, J. Jack
    Hong, David S.
    Eggermont, Alexander M.
    Schilsky, Richard L.
    Mendelsohn, John
    Lazar, Vladimir
    Kurzrock, Razelle
    JOURNAL OF CLINICAL ONCOLOGY, 2014, 32 (15)
  • [30] Participation of African Americans in clinical trials supporting FDA approval of breast cancer medications
    Al Hadidi, Samer
    Mims, Martha
    Miller-Chism, Courtney
    Kamble, Rammurti
    CANCER RESEARCH, 2020, 80 (04)