共 50 条
- [41] Real-world data of Brazilian adults with X-linked hypophosphatemia (XLH) treated with burosumab and comparison with other worldwide cohortsMOLECULAR GENETICS & GENOMIC MEDICINE, 2024, 12 (02):Vaisbich, Maria Helena论文数: 0 引用数: 0 h-index: 0机构: Univ Sao Paulo, Sch Med, Sao Paulo, Brazil Univ Sao Paulo, Sch Med, Rua Eneas Carvalho Aguiar 647, BR-05403000 Sao Paulo, SP, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, Brazilde Cillo, Antonio Cesar Paulillo论文数: 0 引用数: 0 h-index: 0机构: Pontificia Univ Catolica, Campinas, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, BrazilSilva, Barbara Campolina C.论文数: 0 引用数: 0 h-index: 0机构: Univ Ctr Belo Horizonte UNIBH, Hosp Felicio Rocho, Osteometabolism Unit Santa Casa Belo Horizonte, Belo Horizonte, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, BrazilDalva, Catarina Brasil论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Ceara, Fortaleza, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, Brazilde Carvalho, Erico Higino论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Pernambuco, Inst Med Integrada Prof Fernado Figueira, Recife, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, Brazilde Almeida, Juliana M. C. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Pernambuco, Recife, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, BrazilMarques, Larissa L. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Parana, Curitiba, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, BrazilRibeiro, Marcia论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio de Janeiro, Genet Unit, Rio De Janeiro, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, Brazilda Silva, Mauro Borghi M.论文数: 0 引用数: 0 h-index: 0机构: Santa Casa Sao Paulo Sch Med, Endocrinol Unit, Sao Paulo, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, Brazilde Medeiros, Paula Frassinetti V.论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Campina Grande, Campina Grande, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, BrazilMendes, Pedro Henrique论文数: 0 引用数: 0 h-index: 0机构: Inst Fernandes Figueira Fiocruz, Orthoped Unit, Rio De Janeiro, Brazil Univ Sao Paulo, Sch Med, Sao Paulo, Brazil
- [42] Effectiveness of Burosumab Versus Conventional Therapy in Adults With X-Linked Hypophosphatemia in a Real-World Setting From the XLH Disease Monitoring ProgramJOURNAL OF BONE AND MINERAL RESEARCH, 2024, 39 : 172 - 172Florenzano, Pablo论文数: 0 引用数: 0 h-index: 0机构: Pontificia Univ Chile, Santiago, Chile Pontificia Univ Chile, Santiago, ChileImel, Erik A.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN 46202 USA Pontificia Univ Chile, Santiago, ChileKhan, Aliya Aziz论文数: 0 引用数: 0 h-index: 0机构: McMaster Univ, Hamilton, ON, Canada Pontificia Univ Chile, Santiago, ChileJohnson, Ben论文数: 0 引用数: 0 h-index: 0机构: Kyowa Kirin Int, Galashiels, Scotland Pontificia Univ Chile, Santiago, ChileVincent, Marc论文数: 0 引用数: 0 h-index: 0机构: Kyowa Kirin Inc, Bedminster, NJ USA Pontificia Univ Chile, Santiago, ChileNomura, Takanobu论文数: 0 引用数: 0 h-index: 0机构: Pontificia Univ Chile, Santiago, ChileKrolczyk, Stanley论文数: 0 引用数: 0 h-index: 0机构: Kyowa Kirin Co, Tokyo, Japan Pontificia Univ Chile, Santiago, ChileLi, Zhiyi论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx, Tokyo, Japan Pontificia Univ Chile, Santiago, ChileWard, Leanne M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Eastern Ontario, Ottawa, ON, Canada Pontificia Univ Chile, Santiago, Chile
- [43] X-LINKED HYPOPHOSPHATEMIA (XLH) - ABSENCE OF GENDER AND MODE-OF-GENETIC-TRANSMISSION EFFECTS ON DISEASE EXPRESSION IN CHILDRENJOURNAL OF BONE AND MINERAL RESEARCH, 1993, 8 : S292 - S292ARMAMENTOVILLAREAL, R论文数: 0 引用数: 0 h-index: 0机构: WASHINGTON UNIV,SCH MED,DIV BONE & MINERAL DIS,ST LOUIS,MO 63110SCHRANCK, F论文数: 0 引用数: 0 h-index: 0机构: WASHINGTON UNIV,SCH MED,DIV BONE & MINERAL DIS,ST LOUIS,MO 63110WHYTE, MP论文数: 0 引用数: 0 h-index: 0机构: WASHINGTON UNIV,SCH MED,DIV BONE & MINERAL DIS,ST LOUIS,MO 63110
- [44] The effects of burosumab on growth, nephrocalcinosis and cardiovascular outcomes in children with X-linked hypophosphatemia: a single-center experienceJournal of Rare Diseases, 3 (1):Bettyna Olivotto论文数: 0 引用数: 0 h-index: 0机构: Hopital Femme Mere Enfant,Service de Nephrologie, Rhumatologie et Dermatologie Pediatriques, Centre de Reference des Maladies Rares du Calcium et du Phosphore, Filieres Maladies Rares ORKID et OSCAR, BOND et ERKEliane Djatougbé Akolly论文数: 0 引用数: 0 h-index: 0机构: Hopital Femme Mere Enfant,Service de Nephrologie, Rhumatologie et Dermatologie Pediatriques, Centre de Reference des Maladies Rares du Calcium et du Phosphore, Filieres Maladies Rares ORKID et OSCAR, BOND et ERKSara Cabet论文数: 0 引用数: 0 h-index: 0机构: Hopital Femme Mere Enfant,Service de Nephrologie, Rhumatologie et Dermatologie Pediatriques, Centre de Reference des Maladies Rares du Calcium et du Phosphore, Filieres Maladies Rares ORKID et OSCAR, BOND et ERKSacha Flammier论文数: 0 引用数: 0 h-index: 0机构: Hopital Femme Mere Enfant,Service de Nephrologie, Rhumatologie et Dermatologie Pediatriques, Centre de Reference des Maladies Rares du Calcium et du Phosphore, Filieres Maladies Rares ORKID et OSCAR, BOND et ERKAurélia Bertholet-Thomas论文数: 0 引用数: 0 h-index: 0机构: Hopital Femme Mere Enfant,Service de Nephrologie, Rhumatologie et Dermatologie Pediatriques, Centre de Reference des Maladies Rares du Calcium et du Phosphore, Filieres Maladies Rares ORKID et OSCAR, BOND et ERKAurélie de Mul论文数: 0 引用数: 0 h-index: 0机构: Hopital Femme Mere Enfant,Service de Nephrologie, Rhumatologie et Dermatologie Pediatriques, Centre de Reference des Maladies Rares du Calcium et du Phosphore, Filieres Maladies Rares ORKID et OSCAR, BOND et ERKJustine Bacchetta论文数: 0 引用数: 0 h-index: 0机构: Hopital Femme Mere Enfant,Service de Nephrologie, Rhumatologie et Dermatologie Pediatriques, Centre de Reference des Maladies Rares du Calcium et du Phosphore, Filieres Maladies Rares ORKID et OSCAR, BOND et ERK
- [45] Health-related Quality of Life of Children with X-linked Hypophosphatemia in Germany in the Burosumab EraPEDIATRIC NEPHROLOGY, 2024, 39 (01) : S266 - S266Boeckmann, Ineke论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyKlein, Martin论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Appl Sci North Rhine Westphalia, Dept Social Sci, Cologne, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyObermaier, Michael论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Appl Sci North Rhine Westphalia, Dept Social Sci, Cologne, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyMutze, Helena论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Appl Sci North Rhine Westphalia, Dept Social Sci, Cologne, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyWilden, Sophia论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Appl Sci North Rhine Westphalia, Dept Social Sci, Cologne, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyRehberg, Mirko论文数: 0 引用数: 0 h-index: 0机构: Univ Cologne, Fac Med, Dept Pediat, Cologne, Germany Univ Cologne, Univ Hosp Cologne, Dept Pediat, Cologne, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanySchlingmann, Karl论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp, Dept Gen Pediat, Pediat Nephrol, Munster, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyMetzing, Oliver论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp, Dept Gen Pediat & Pediat Endocrinol, Jena, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyKemper, Markus论文数: 0 引用数: 0 h-index: 0机构: Asklepios Childrens Hosp Hamburg Heidberg, Dept Pediat, Pediat Nephrol, Hamburg, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyWeitz, Marcus论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Heidelberg, Dept Pediat 1, Heidelberg, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyWuehl, Elke论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Ctr Pediat & Adolescent Med, Div Pediat, Heidelberg, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyPatzer, Ludwig论文数: 0 引用数: 0 h-index: 0机构: St Elisabeth & St Barbara Childrens Hosp, Halle, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyZivicnjak, Miroslav论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanySchnabel, Dirk论文数: 0 引用数: 0 h-index: 0机构: Univ Med, Charite Berlin, Ctr Chronically Sick Children, Pediat Endocrinol, Berlin, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, GermanyHaffner, Dieter论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, Germany Hannover Med Sch, Dept Pediat Kidney Liver & Metab Dis, Hannover, Germany
- [46] Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked HypophosphatemiaJOURNAL OF CLINICAL ENDOCRINOLOGY & METABOLISM, 2022, 107 (08): : E3241 - E3253Ward, Leanne M.论文数: 0 引用数: 0 h-index: 0机构: Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, Canada Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaGlorieux, Francis H.论文数: 0 引用数: 0 h-index: 0机构: McGill Univ, Shriners Hosp Children, Montreal, PQ H4A OA9, Canada Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaWhyte, Michael P.论文数: 0 引用数: 0 h-index: 0机构: Shriners Hosp Children St Louis, St Louis, MO 63110 USA Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaMunns, Craig F.论文数: 0 引用数: 0 h-index: 0机构: Univ Queensland, Child Hlth Res Ctr, Brisbane, Qld 4072, Australia Queensland Childrens Hosp, Dept Endocrinol & Diabet, Brisbane, Qld, Australia Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaPortale, Anthony A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Pediat, San Francisco, CA 94143 USA Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaHoegler, Wolfgang论文数: 0 引用数: 0 h-index: 0机构: Johannes Kepler Univ Linz, Dept Pediat & Adolescent Med, A-4040 Linz, Austria Univ Birmingham, Inst Metab & Syst Res, Birmingham B15 2TT, W Midlands, England Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaSimmons, Jill H.论文数: 0 引用数: 0 h-index: 0机构: Vanderbilt Univ, Div Endocrinol & Diabet, Dept Pediat, Sch Med, Nashville, TN 63110 USA Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaGottesman, Gary S.论文数: 0 引用数: 0 h-index: 0机构: Shriners Hosp Children St Louis, St Louis, MO 63110 USA Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaPadidela, Raja论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Dept Paediat Endocrinol, Manchester M13 9WL, Lancs, England Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, Canada论文数: 引用数: h-index:机构:Cheong, Hae Il论文数: 0 引用数: 0 h-index: 0机构: Osaka Univ, Grad Sch Med, Osaka 5530003, Japan Tottori Univ, Div Pediat & Perinatol, Fac Med, Yonago, Japan Seoul Natl Univ, Dept Pediat, Childrens Hosp, Seoul 14068, South Korea Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaNilsson, Ola论文数: 0 引用数: 0 h-index: 0机构: Karolinska Inst, Div Pediat Endocrinol, S-17177 Stockholm, Sweden Karolinska Inst, Ctr Mol Med, S-17177 Stockholm, Sweden Orebro Univ, Dept Pediat, Sch Med Sci, S-70362 Orebro, Sweden Univ Hosp, S-70362 Orebro, Sweden Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaMao, Meng论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx Pharmaceut Inc, Novato, CA 94949 USA Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaChen, Angel论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx Pharmaceut Inc, Novato, CA 94949 USA Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaSkrinar, Alison论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx Pharmaceut Inc, Novato, CA 94949 USA Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaRoberts, Mary Scott论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx Pharmaceut Inc, Novato, CA 94949 USA Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, CanadaImel, Erik A.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ, Sch Med, Dept Med, Indianapolis, IN 46202 USA Indiana Univ, Sch Med, Dept Pediat, Indianapolis, IN 46202 USA Univ Ottawa, Dept Pediat, Fac Med, Ottawa, ON K1H 8L1, Canada
- [47] Newly Diagnosed Hyperparathyroidism After 3 Years Of Burosumab In Children Affected With X-Linked HypophosphatemiaJOURNAL OF BONE AND MINERAL RESEARCH, 2023, 38 : 433 - 433Zhukouskaya, Volha论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, France FHU DDS Net, Sch Dent, Montrouge, France Plateforme dImagerie Vivant PIV, Montrouge, France Hop Cochin, APHP, Paris, France Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, FranceErtl, Alexandra论文数: 0 引用数: 0 h-index: 0机构: Bicetre Paris Saclay Hosp, AP HP, Reference Ctr rare Dis Calcium & Phosphate Metab, Endocrinol & Diabet children,DMU SEA,OSCAR filier, Paris, France Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, FranceBerkenou, Jugurtha论文数: 0 引用数: 0 h-index: 0机构: Bicetre Paris Saclay Hosp, AP HP, Reference Ctr rare Dis Calcium & Phosphate Metab, Endocrinol & Diabet children,DMU SEA,OSCAR filier, Paris, France Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, FranceAudrain, Christelle论文数: 0 引用数: 0 h-index: 0机构: Bicetre Paris Saclay Hosp, AP HP, Reference Ctr rare Dis Calcium & Phosphate Metab, Endocrinol & Diabet children,DMU SEA,OSCAR filier, Paris, France Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, FranceBardet, Claire论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, France FHU DDS Net, Sch Dent, Montrouge, France Plateforme dImagerie Vivant PIV, Montrouge, France Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, FranceChaussain, Catherine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, France FHU DDS Net, Sch Dent, Montrouge, France Plateforme dImagerie Vivant PIV, Montrouge, France Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, FranceRothenbuhler, Anya论文数: 0 引用数: 0 h-index: 0机构: Bicetre Paris Saclay Hosp, AP HP, Reference Ctr rare Dis Calcium & Phosphate Metab, Endocrinol & Diabet children,DMU SEA,OSCAR filier, Paris, France Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, FranceLinglart, Agnes论文数: 0 引用数: 0 h-index: 0机构: Bicetre Paris Saclay Hosp, AP HP, Reference Ctr rare Dis Calcium & Phosphate Metab, Endocrinol & Diabet children,DMU SEA,OSCAR filier, Paris, France Univ Paris Cite, Lab Orofacial Pathol Imaging & Biotherapies, URP2496, Montrouge, France
- [48] Combined Treatment With Leuprolide Acetate and Burosumab in X-linked Hypophosphatemia and Precocious Puberty: A Therapeutic ResponseAACE CLINICAL CASE REPORTS, 2025, 11 (01): : 18 - 23Penna, Gustavo Tempone Cardoso论文数: 0 引用数: 0 h-index: 0机构: Ctr Univ Sao Camilo, Fac Med, Ave Nazare, Sao Paulo, SP, Brazil Ctr Univ Sao Camilo, Fac Med, Ave Nazare, Sao Paulo, SP, BrazilFigueiredo, Carolina Costa论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Darcy Vargas, Rua Dr Serafico de Assis Carvalho, Sao Paulo, SP, Brazil Ctr Univ Sao Camilo, Fac Med, Ave Nazare, Sao Paulo, SP, BrazilEvangelista, Nara Michelle de Araujo论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Darcy Vargas, Rua Dr Serafico de Assis Carvalho, Sao Paulo, SP, Brazil Ctr Univ Sao Camilo, Fac Med, Ave Nazare, Sao Paulo, SP, BrazilFernandes, Vania de Fatima Tonetto论文数: 0 引用数: 0 h-index: 0机构: Ctr Univ Sao Camilo, Fac Med, Ave Nazare, Sao Paulo, SP, Brazil Ctr Univ Sao Camilo, Fac Med, Ave Nazare, Sao Paulo, SP, BrazilSalmona, Patricia论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Darcy Vargas, Rua Dr Serafico de Assis Carvalho, Sao Paulo, SP, Brazil Ctr Univ Sao Camilo, Fac Med, Ave Nazare, Sao Paulo, SP, BrazilNeto, Guido de Paula Colares论文数: 0 引用数: 0 h-index: 0机构: Ctr Univ Sao Camilo, Fac Med, Ave Nazare, Sao Paulo, SP, Brazil Ctr Univ Sao Camilo, Fac Med, Ave Nazare, Sao Paulo, SP, Brazil
- [49] High bone mineral apparent density in children with X-linked hypophosphatemiaOSTEOPOROSIS INTERNATIONAL, 2013, 24 (08) : 2215 - 2221Beck-Nielsen, S. S.论文数: 0 引用数: 0 h-index: 0机构: Univ Southern Denmark, Inst Clin Res, DK-5000 Odense C, Denmark Hosp Southwest Denmark, Dept Pediat, DK-6700 Esbjerg, Denmark Univ Southern Denmark, Inst Clin Res, DK-5000 Odense C, DenmarkBrixen, K.论文数: 0 引用数: 0 h-index: 0机构: Univ Southern Denmark, Inst Clin Res, DK-5000 Odense C, Denmark Odense Univ Hosp, Dept Endocrinol, DK-5000 Odense C, Denmark Univ Southern Denmark, Inst Clin Res, DK-5000 Odense C, DenmarkGram, J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Southwest Denmark, Dept Endocrinol, DK-6700 Esbjerg, Denmark Univ Southern Denmark, Inst Clin Res, DK-5000 Odense C, DenmarkMolgaard, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Southern Denmark, Inst Clin Res, DK-5000 Odense C, Denmark Univ Copenhagen, Fac Sci, Dept Nutr Exercise & Sports, DK-1958 Copenhagen, Denmark Univ Southern Denmark, Inst Clin Res, DK-5000 Odense C, Denmark
- [50] Burosumab Improved Rickets, Phosphate Metabolism, and Clinical Outcomes Compared to Conventional Therapy in Children with X-Linked Hypophosphatemia (XLH) - A Randomized Controlled Phase 3 StudyHORMONE RESEARCH IN PAEDIATRICS, 2018, 90 : 57 - 58Nilsson, Ola论文数: 0 引用数: 0 h-index: 0机构: Karolinska Inst, Stockholmn, WI USA Orebro Univ, Orebro, Sweden Karolinska Inst, Stockholmn, WI USAWhyte, Michael P.论文数: 0 引用数: 0 h-index: 0机构: Shriners Hosp Children, St Louis, MO USA Karolinska Inst, Stockholmn, WI USAImel, Erik A.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN 46202 USA Karolinska Inst, Stockholmn, WI USAMunns, Craig论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Westmead, Sydney, NSW, Australia Karolinska Inst, Stockholmn, WI USAPortale, Anthony A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, San Francisco, CA 94143 USA Karolinska Inst, Stockholmn, WI USAWard, Leanne论文数: 0 引用数: 0 h-index: 0机构: Univ Ottawa, Ottawa, ON, Canada Karolinska Inst, Stockholmn, WI USASimmons, Jill H.论文数: 0 引用数: 0 h-index: 0机构: Vanderbilt Univ, Sch Med, Nashville, TN 37212 USA Karolinska Inst, Stockholmn, WI USAPadidela, Raja论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Karolinska Inst, Stockholmn, WI USA论文数: 引用数: h-index:机构:Cheong, Hae Il论文数: 0 引用数: 0 h-index: 0机构: Seoul Natl Univ, Childrens Hosp, Seoul, South Korea Karolinska Inst, Stockholmn, WI USAMao, Meng论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx Pharmaceut Inc, Novato, CA USA Karolinska Inst, Stockholmn, WI USASkrinar, Alison论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx Pharmaceut Inc, Novato, CA USA Karolinska Inst, Stockholmn, WI USAChen, Chao-Yin论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx Pharmaceut Inc, Novato, CA USA Karolinska Inst, Stockholmn, WI USAMartin, Javier San论文数: 0 引用数: 0 h-index: 0机构: Ultragenyx Pharmaceut Inc, Novato, CA USA Karolinska Inst, Stockholmn, WI USAGlorieux, Francis论文数: 0 引用数: 0 h-index: 0机构: McGill Univ, Shriners Hosp Children Canada, Montreal, PQ, Canada Karolinska Inst, Stockholmn, WI USA