Effects of burosumab treatment on mineral homeostasis in children and adolescents with X-linked hypophosphatemia: lessons from the German XLH Registry

被引:0
|
作者
Ewert, Annika [1 ]
Rehberg, Mirko [2 ]
Schlingmann, Karl Peter [3 ]
Kemper, Markus [4 ]
Patzer, Ludwig [5 ]
John, Ulrike [6 ]
Metzing, Oliver [6 ]
Staude, Hagen [7 ]
Weitz, Marcus [8 ]
Wuehl, Elke [9 ,10 ]
Schaefer, Franz [9 ,10 ]
Freiberg, Clemens [11 ]
Hiort, Olaf [12 ]
Schnabel, Dirk [13 ]
Haffner, Dieter [1 ]
机构
[1] Hannover Med Sch, Dept Pediat Nephrol, Hannover, Germany
[2] Univ Cologne, Dept Pediat, Cologne, Germany
[3] Univ Childrens Hosp, Dept Gen Pediat Pediat Nephrol, Munster, Germany
[4] Asklepios Childrens Hosp Hamburg Heidberg, Pediat, Hamburg, Germany
[5] St Elisabeth & St Barbara Childrens Hosp, Pediat, Halle, Germany
[6] Univ Childrens Hosp, Pediat Nephrol, Jena, Germany
[7] Univ Childrens Hosp, Pediat Nephrol, Rostock, Germany
[8] Univ Childrens Hosp, Pediat Nephrol, Tubingen, Germany
[9] Univ Heidelberg Hosp, Div Pediat Nephrol, Heidelberg, Germany
[10] Ctr Pediat & Adolescent Med, Heidelberg, Germany
[11] Univ Med Gottingen, Dept Pediat, Gottingen, Germany
[12] Univ Childrens Hosp Lubeck, Pediat, Lubeck, Germany
[13] Univ Med Charite, Ctr Chronically Sick Children Pediat Endocrinol, Berlin, Germany
关键词
D O I
暂无
中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
O-19
引用
收藏
页码:2264 / 2265
页数:2
相关论文
共 50 条
  • [1] Effects of burosumab treatment on mineral homeostasis in children and adolescents with X-linked hypophosphatemia: lessons from the German XLH Registry
    Ewert, Annika
    Rehberg, Mirko
    Hiort, Olaf
    Binder, Gerhard
    Schroeder, Carmen
    Jorch, Norbert
    Richter-Unruh, Annette
    Freiberg, Clemens
    Schlingmann, Karl Peter
    Haffner, Dieter
    Schnabel, Dirk
    HORMONE RESEARCH IN PAEDIATRICS, 2022, 95 (SUPPL 2): : 30 - 31
  • [2] EFFECTS OF BUROSUMAB TREATMENT ON MINERAL HOMEOSTASIS IN CHILDREN AND ADOLESCENTS WITH X-LINKED HYPOPHOSPHATEMIA: LESSONS FROM THE GERMAN XLH REGISTRY
    Mirko, Ewert Annika Rehberg
    Peter, Schlingmann Karl
    Markus, Kemper
    Ute, Derichs
    Ludwig, Patzer
    Hagen, Staude
    Ulrike, John
    Oliver, Metzing
    Marcus, Weitz
    Clemens, Freiberg
    Elke, Wuehl
    Franz, Schaefer
    Olaf, Hiort
    Dirk, Schnabel
    Dieter, Haffner
    PEDIATRIC NEPHROLOGY, 2022, 37 (11) : 2814 - 2815
  • [3] Effects of Burosumab Treatment on Mineral Metabolism in Children and Adolescents With X-linked Hypophosphatemia
    Ewert, Annika
    Rehberg, Mirko
    Schlingmann, Karl Peter
    Hiort, Olaf
    John-Kroegel, Ulrike
    Metzing, Oliver
    Wuehl, Elke
    Schaefer, Franz
    Kemper, Markus J.
    Derichs, Ute
    Richter-Unruh, Annette
    Patzer, Ludwig
    Albers, Norbert
    Dunstheimer, Desiree
    Haberland, Holger
    Heger, Sabine
    Schroeder, Carmen
    Jorch, Norbert
    Schmid, Elmar
    Staude, Hagen
    Weitz, Marcus
    Freiberg, Clemens
    Leifheit-Nestler, Maren
    Zivicnjak, Miroslav
    Schnabel, Dirk
    Haffner, Dieter
    JOURNAL OF CLINICAL ENDOCRINOLOGY & METABOLISM, 2023, 108 (10): : E998 - E1006
  • [4] Impact of stopping burosumab treatment at the end of skeletal growth in adolescents with X-linked hypophosphatemia (XLH)
    Jarvis, Charlotte
    Ramakrishnan, Renuka
    Dharmaraj, Poonam
    Mushtaq, Talat
    Gupta, Sanjay
    Williams, Angela
    Rylands, Angela J.
    Barham, Helen
    Nixon, Annabel
    Uday, Suma
    BONE REPORTS, 2025, 24
  • [5] Burosumab Therapy in Children with X-Linked Hypophosphatemia
    Carpenter, Thomas O.
    Whyte, Michael P.
    Imel, Erik A.
    Boot, Annemieke M.
    Hogler, Wolfgang
    Linglart, Agnes
    Padidela, Raja
    van't Hoff, William
    Mao, Meng
    Chen, Chao-Yin
    Skrinar, Alison
    Kakkis, Emil
    San Martin, Javier
    Portale, Anthony A.
    NEW ENGLAND JOURNAL OF MEDICINE, 2018, 378 (21): : 1987 - 1998
  • [6] The International X-Linked Hypophosphatemia (XLH) Registry: Overview of the Dataset
    Nilsson, Ola
    Liu, Jonathan
    Williams, Angela
    Wood, Sue
    JOURNAL OF BONE AND MINERAL RESEARCH, 2023, 38 : 287 - 287
  • [7] Burosumab and Dental Abscesses in Children With X-Linked Hypophosphatemia
    Gadion, Margaux
    Herve, Agathe
    Herrou, Julia
    Rothenbuhler, Anya
    Smail-Faugeron, Violaine
    Courson, Frederic
    Linglart, Agnes
    Chaussain, Catherine
    Duplan, Martin Biosse
    JBMR PLUS, 2022, 6 (11)
  • [8] Clinical Evidence for the Benefits of Burosumab Therapy for X-Linked Hypophosphatemia (XLH) and Other Conditions in Adults and Children
    Schindeler, Aaron
    Biggin, Andrew
    Munns, Craig F.
    FRONTIERS IN ENDOCRINOLOGY, 2020, 11
  • [9] X-LINKED HYPOPHOSPHATEMIA (XLH): DIAGNOSIS AND TREATMENT IN ADULTS
    Medina, A.
    AGING CLINICAL AND EXPERIMENTAL RESEARCH, 2023, 35 : S119 - S120
  • [10] Diagnosis, treatment-monitoring and follow-up of children and adolescents with X-linked hypophosphatemia (XLH)
    Rothenbuhler, Anya
    Schnabel, Dirk
    Hogler, Wolfgang
    Linglart, Agnes
    METABOLISM-CLINICAL AND EXPERIMENTAL, 2020, 103