LUMASIRAN TREATMENT IMMEDIATELY AFTER BIRTH IN PRIMARY HYPEROXALURIA TYPE 1: NEVER TOO SOON

被引:0
|
作者
Peruzzi, Licia [1 ]
Leporati, Marta [2 ]
Petrarulo, Michele [2 ]
Martins, Vitor Dias [1 ]
Coscia, Alessandra [3 ]
Marozio, Luca [4 ]
Camilla, Roberta [1 ]
Mattozzi, Francesca [1 ]
Gianoglio, Bruno [1 ]
机构
[1] Regina Margherita Childrens Hosp, Pediat Nephrol Turin, Regina, SK, Italy
[2] Osped Mauriziano Umberto 1, Analyt Chem & Kidney Stone Dis Unit, Lab Anal, Turin, Italy
[3] Univ Turin, Neonatal Intens Care Unit, Turin, Italy
[4] Univ Turin, Obstet & Gynecol, Turin, Italy
关键词
D O I
暂无
中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
Fr-P 151
引用
收藏
页码:S198 / S199
页数:2
相关论文
共 50 条
  • [21] RESPONSE TO LUMASIRAN IN PRIMARY HYPEROXALURIA TYPE 1 (PH1): FIRST CLINICAL EXPERIENCES
    Saffe, Sina
    Kemper, Markus J.
    Hansen, Matthias
    Kanzelmeyer, Nele
    Buescher, Anja
    Oh, Jun
    Doerry, Katja
    PEDIATRIC NEPHROLOGY, 2022, 37 (11) : 2854 - 2854
  • [22] STABLE EGFR IN PATIENTS WITH PRIMARY HYPEROXALURIA TYPE 1 TREATED WITH LUMASIRAN, REGARDLESS OF KIDNEY FUNCTION AT START OF TREATMENT
    Hayes, Wesley
    Garrelfs, Sander
    Sas, David
    Lieske, John
    Ngo, Taylor
    Gansner, John
    McGregor, Tracy
    Frishberg, Yaacov
    NEPHROLOGY DIALYSIS TRANSPLANTATION, 2021, 36 : 113 - 113
  • [23] Relationship of baseline weight and response to lumasiran in patients with primary hyperoxaluria type 1 on hemodialysis
    Michael, Mini
    Groothoff, Jaap
    Shasha-Lavsky, Hadas
    Lieske, John
    Yaacov, Frishberg
    Simkova, Eva
    Sellier-Leclerc, Anne-Laure
    Devresse, Arnaud
    Guebre-Egziabher, Fitsum
    Bakkaloglu, Sevcan
    Mourani, Chebl
    Saqan, Rola
    Singer, Richard
    Gansner, John
    Magen, Daniella
    PEDIATRIC NEPHROLOGY, 2023, 38 (07) : 2293 - 2293
  • [24] Case Report: effect of lumasiran treatment in a late preterm baby with antenatal diagnosis of primary hyperoxaluria type 1
    Taroni, Francesca
    Berrettini, Alfredo
    Gnech, Michele
    Rella, Francesca
    Manzoni, Gian Antonio
    Montini, Giovanni
    FRONTIERS IN PEDIATRICS, 2024, 11
  • [25] Multicenter Long-Term Real World Data on Treatment With Lumasiran in Patients With Primary Hyperoxaluria Type 1
    Martin-Higueras, Cristina
    Borghese, Lodovica
    Torres, Armando
    Fraga-Bilbao, Fatima
    Santana-Estupinan, Raquel
    Stefanidis, Constantinos J.
    Tory, Kalman
    Walli, Adam
    Gondra, Leire
    Kempf, Caroline
    Gessner, Michaela
    Habbig, Sandra
    Eifler, Lisa
    Schmitt, Claus P.
    Ruedel, Benjamin
    Bartram, Malte P.
    Beck, Bodo B.
    Hoppe, Bernd
    KIDNEY INTERNATIONAL REPORTS, 2023, 9 (01): : 114 - 133
  • [26] Glycolate oxidase inhibition by lumasiran varies between patients with primary hyperoxaluria type 1
    Garrelfs, Sander F.
    Metry, Elisabeth L.
    van Harskamp, Dewi
    Vaz, Frederic M.
    van den Akker, Chris H. P.
    Schierbeek, Henk
    Groothoff, Jaap W.
    Oosterveld, Michiel J. S.
    KIDNEY INTERNATIONAL, 2023, 103 (05) : 990 - 993
  • [27] Less Is More: A Case of Isolated Kidney Transplantation with Lumasiran in Primary Hyperoxaluria Type 1
    Ice, Alissa Angelica
    Azam, Muhammad Jibran
    Langone, Anthony J.
    JOURNAL OF THE AMERICAN SOCIETY OF NEPHROLOGY, 2024, 35 (10):
  • [28] IMPACT OF BASELINE URINARY OXALATE ON RESPONSE TO LUMASIRAN IN PATIENTS WITH PRIMARY HYPEROXALURIA TYPE 1
    Sas, David
    Bacchetta, Justine
    Ngo, Taylor
    Gansner, John
    Brown, Thomas
    Garrelfs, Sander
    AMERICAN JOURNAL OF KIDNEY DISEASES, 2022, 79 (04) : S9 - S9
  • [29] Case Report: Sustained Efficacy of Lumasiran at 18 Months in Primary Hyperoxaluria Type 1
    Chiodini, Benedetta
    Tram, Nathalie
    Adams, Brigitte
    Hennaut, Elise
    Lolin, Ksenija
    Ismaili, Khalid
    FRONTIERS IN PEDIATRICS, 2022, 9
  • [30] Phase 1/2 Study of Lumasiran for Treatment of Primary Hyperoxaluria Type 1 A Placebo-Controlled Randomized Clinical Trial
    Frishberg, Yaacov
    Deschenes, Georges
    Groothoff, Jaap W.
    Hulton, Sally-Anne
    Magen, Daniella
    Harambat, Jerome
    van't Hoff, William G.
    Lorch, Ulrike
    Milliner, Dawn S.
    Lieske, John C.
    Haslett, Patrick
    Garg, Pushkal P.
    Vaishnaw, Akshay K.
    Talamudupula, Sandeep
    Lu, Jiandong
    Habtemariam, Bahru A.
    Erbe, David, V
    McGregor, Tracy L.
    Cochat, Pierre
    CLINICAL JOURNAL OF THE AMERICAN SOCIETY OF NEPHROLOGY, 2021, 16 (07): : 1025 - 1036