LONG TERM SAFETY AND EFFICACY OF CAR-T CELL TREATMENT IN REFRACTORY SYSTEMIC LUPUS ERYTHEMATOSUS - DATA FROM THE FIRST SEVEN PATIENTS

被引:6
|
作者
Taubmann, J. [1 ,2 ,3 ,4 ]
Mueller, F. [2 ,3 ,4 ,5 ]
Boeltz, S. [1 ,2 ,3 ,4 ]
Voelkl, S. [2 ,3 ,4 ,5 ]
Aigner, M. [2 ,3 ,4 ,5 ]
Kleyer, A. [1 ,2 ,3 ,4 ]
Minnopoulou, I. [1 ,2 ,3 ,4 ]
Locatelli, F. [6 ]
D'agostino, M. A. [7 ]
Gary, R. [2 ,3 ,4 ,5 ]
Krestchmann, S. [2 ,3 ,4 ,5 ]
Kharboutli, S. [2 ,3 ,4 ,5 ]
Mougiakakos, D. [2 ,3 ,4 ,5 ,8 ]
Kroenke, G. [1 ,2 ,3 ,4 ]
Andreas, M. [2 ,3 ,4 ,5 ]
Schett, G. [1 ,2 ,3 ,4 ]
机构
[1] Univ Klinikum Erlangen Nurnberg, Dept Internal Med 3 Rheumatol & Immunol, Erlangen, Germany
[2] Friedrich Alexander Univ Erlangen Nurnberg, Erlangen, Germany
[3] Friedrich Alexander Univ Erlangen Nuremberg, Deutsch Zentrum Immuntherapie DZI, Erlangen, Germany
[4] Univ Klinikum Erlangen, Erlangen, Germany
[5] Univ Klinikum Erlangen Nurnberg, Dept Internal Med 5 Hematol & Oncol, Erlangen, Germany
[6] Osped Pediat Bambino Gesu, Dept Pediat Onco Hematol & Transfus Med, Bambino Gesu, Rome, Italy
[7] Catholica Univ, Div Rheumatol, Fdn Policlin Univ A Gemelli, Sacred Heart, Rome, Italy
[8] Univ Klin Hamatol & Onkol, Hamatol & Onkol, Univ Klinikum Magdeburg AoR, Magdeburg, Germany
关键词
Systemic lupus erythematosus; Remission; Treat to target;
D O I
10.1136/annrheumdis-2023-eular.3736
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
OP0141
引用
收藏
页码:93 / 94
页数:2
相关论文
共 50 条
  • [1] CAR-T CELL TREATMENT OF REFRACTORY SYSTEMIC LUPUS ERYTHEMATOSUS- SAFETY AND PRELIMINARY EFFICACY DATA FROM THE FIRST FOUR PATIENTS
    Schett, G.
    Boeltz, S.
    Mueller, F.
    Kleyer, A.
    Voelkl, S.
    Aigner, M.
    Gary, R.
    Kretschmann, S.
    Simon, D.
    Kharboutli, S.
    Mougiakakos, D.
    Kroenke, G.
    Andreas, M.
    ANNALS OF THE RHEUMATIC DISEASES, 2022, 81 : 185 - 185
  • [2] CD19-Targeted CAR-T Cells in Refractory Systemic Lupus Erythematosus: Safety, Efficacy, and Mechanistic Insights from the First Five Patients
    Mueller, Fabian
    Voelkl, Simon
    Mougiakakos, Dimitrios
    Boeltz, Sebastian
    Aigner, Michael
    Gary, Regina
    Kretschmann, Sascha
    Kharboutli, Soraya
    Kleyer, Arnd
    Simon, David
    Roesler, Wolf
    Habenicht, Katharina M.
    Winkler, Thomas H.
    Kroenke, Gerhard
    Schett, Georg
    Mackensen, Andreas
    BLOOD, 2022, 140 : 4562 - 4563
  • [3] CAR T Cell Treatment of Refractory Systemic Lupus Erythematosus
    Schett, Georg
    Boeltz, Sebastian
    Mueller, Fabian
    Kleyer, Arnd
    Voelkl, Simon
    Aigner, Michael
    Gary, Regina
    Kretschmann, Sascha
    Simon, David
    Kharboutli, Soraya
    Mougiakakos, Dimitrios
    Kroenke, Gerhard
    Mackensen, Andreas
    ARTHRITIS & RHEUMATOLOGY, 2022, 74 : 3284 - 3285
  • [4] CD19/BCMA CAR-T Cell Therapy for Refractory Systemic Lupus Erythematosus - Safety and Preliminary Efficacy Data from a Phase I Clinical Study
    Feng, Jingjing
    Hu, Yongxian
    Chang, Alex H.
    Huang, He
    BLOOD, 2023, 142
  • [5] CAR-T cell therapy: new hope for systemic lupus erythematosus patients
    Jin, Xuexiao
    Han, Yongmei
    Wang, James Q.
    Lu, Linrong
    CELLULAR & MOLECULAR IMMUNOLOGY, 2021, 18 (12) : 2581 - 2582
  • [6] CAR-T cell therapy: new hope for systemic lupus erythematosus patients
    Xuexiao Jin
    Yongmei Han
    James Q. Wang
    Linrong Lu
    Cellular & Molecular Immunology, 2021, 18 : 2581 - 2582
  • [7] LONG TERM EFFICACY AND SAFETY OF TACROLIMUS FOR PATIENTS WITH SYSTEMIC LUPUS ERYTHEMATOSUS
    Mukai, M.
    Kondo, M.
    Kataoka, H.
    CLINICAL AND EXPERIMENTAL RHEUMATOLOGY, 2016, 34 (04) : S78 - S78
  • [8] Long-term efficacy and safety of rituximab in refractory and relapsing systemic lupus erythematosus
    Catapano, Fausta
    Chaudhry, Afzal N.
    Jones, Rachel B.
    Smith, Kenneth G. C.
    Jayne, David W.
    NEPHROLOGY DIALYSIS TRANSPLANTATION, 2010, 25 (11) : 3586 - 3592
  • [9] FIRST EVIDENCE FOR EFFICACY OF CAR-T CELL TREATMENT IN REFRACTORY ANTISYNTHETASE SYNDROME
    Taubmann, J.
    Mueller, F.
    Boeltz, S.
    Knitza, J.
    Voelkl, S.
    Aigner, M.
    Kleyer, A.
    Minnopoulou, I.
    Locatelli, F.
    D'agostino, M. A.
    Gary, R.
    Krestchmann, S.
    Kharboutli, S.
    Mougiakakos, D.
    Kroenke, G.
    Andreas, M.
    Schett, G.
    ANNALS OF THE RHEUMATIC DISEASES, 2023, 82 : 957 - 958
  • [10] Efficacy and Safety of Car-T-Cell Treatment in Refractory Antisynthetase Syndrome - Data of the First Three Patients
    Taubmann, Jule
    Knitza, Johannes
    Mueller, Fabian
    Boeltz, Sebastian
    Voelkl, Simon
    Aigner, Michael
    Kleyer, Arnd
    Minnopoulou, Ioanna
    Gary, Regina
    Kretschmann, Sascha
    Mackensen, Andreas
    Schett, Georg
    ARTHRITIS & RHEUMATOLOGY, 2023, 75 : 4884 - 4886