The Use of Onasemnogene-abeparvovec at 33 weeks' gestation in Spinal Muscular Atrophy with One Copy of SMN2

被引：1
|
作者：
Ajjarapu, Aparna [1 ]
Ramachandra, Divya [2 ]
Mathews, Katherine [1 ]
机构：
[1] Univ Iowa, Carver Coll Med, Dept Neurol, Iowa City, IA USA
[2] Advocate Childrens Hosp, Dept Genet, Park Ridge, IL USA
来源：
NEUROLOGY | 2023年 / 100卷 / 17期
关键词：
D O I：
10.1212/WNL.0000000000203032
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P2-8.013
引用
收藏
页数：3
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