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- [31] Targeting a6GABAA receptors as a novel therapy for schizophrenia: A proof-of-concept preclinical study using various animal modelsBIOMEDICINE & PHARMACOTHERAPY, 2022, 150Lee, Ming Tatt论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, Taiwan UCSI Univ, Fac Pharmaceut Sci, Kuala Lumpur 56000, Malaysia Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, Taiwan论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Lee, Hsin-Jung论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, Taiwan Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, TaiwanChang, Man-Hsin论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, Taiwan Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, TaiwanWu, Chen-Yi论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, Taiwan Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, TaiwanKnutson, Daniel E.论文数: 0 引用数: 0 h-index: 0机构: Univ Wisconsin Milwaukee, Dept Chem & Biochem, Milwaukee, WI 53211 USA Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, TaiwanMihovilovic, Marko论文数: 0 引用数: 0 h-index: 0机构: TU Wien, Inst Appl Synthet Chem, A-1060 Vienna, Austria Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, TaiwanCook, James论文数: 0 引用数: 0 h-index: 0机构: Univ Wisconsin Milwaukee, Dept Chem & Biochem, Milwaukee, WI 53211 USA Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, Taiwan论文数: 引用数: h-index:机构:Nabeshima, Toshitaka论文数: 0 引用数: 0 h-index: 0机构: Fujita Hlth Univ, Grad Sch Hlth Sci, Adv Diagnost Syst Res Lab, Toyoake, Aichi 4701192, Japan Japanese Drug Org Appropriate Use & Res, Toyoake, Aichi 4680069, Japan Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, TaiwanChiou, Lih-Chu论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, Taiwan Natl Taiwan Univ, Grad Inst Brain & Mind Sci, Coll Med, Taipei 10051, Taiwan China Med Univ, Grad Inst Acupuncture Sci, Taichung 40402, Taiwan Natl Taiwan Univ, Grad Inst Pharmacol, Coll Med, 1 Jen-Ai Rd,Sect 1, Taipei 100, Taiwan Natl Taiwan Univ, Dept & Grad Inst Pharmacol, Coll Med, Taipei 10051, Taiwan
- [32] Preclinical Proof-of-Concept: A Novel Hybrid Gene Therapy Approach to Treat Severe Early-Onset Ornithine Transcarbamylase DeficiencyMOLECULAR THERAPY, 2023, 31 (04) : 68 - 69Kok, Bernard论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USAEbeid, David论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USAMishgin, Nairika论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USALoveless, Ryan论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USAHajj, Khal论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USANguyen, Tuyen论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USADeng, Christopher论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USAGriffin, Peter论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USALi, Mu论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USABennett, Michael论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USABattiprolu, Pavan论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USAWarner, Brent论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USAMadison, Blair论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USARychak, Joshua论文数: 0 引用数: 0 h-index: 0机构: Poseida Therapeut, San Diego, CA USA Poseida Therapeut, In Vivo Gene Therapy, San Diego, CA USA
- [33] G2C4 targeting antisense oligonucleotides potently mitigate TDP-43 dysfunction in human C9orf72 ALS/FTD induced pluripotent stem cell derived neuronsActa Neuropathologica, 2024, 147Jeffrey D. Rothstein论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science InstituteVictoria Baskerville论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science InstituteSampath Rapuri论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science InstituteEmma Mehlhop论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science InstitutePaymaan Jafar-Nejad论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science InstituteFrank Rigo论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science InstituteFrank Bennett论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science InstituteSarah Mizielinska论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science InstituteAdrian Isaacs论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science InstituteAlyssa N. Coyne论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins University School of Medicine,Brain Science Institute
- [34] G2C4 targeting antisense oligonucleotides potently mitigate TDP-43 dysfunction in human C9orf72 ALS/FTD induced pluripotent stem cell derived neuronsACTA NEUROPATHOLOGICA, 2024, 147 (01)Rothstein, Jeffrey D.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USABaskerville, Victoria论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USARapuri, Sampath论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USAMehlhop, Emma论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USAJafar-Nejad, Paymaan论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA 92010 USA Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USARigo, Frank论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA 92010 USA Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USABennett, Frank论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA 92010 USA Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USAMizielinska, Sarah论文数: 0 引用数: 0 h-index: 0机构: Kings Coll London, UK Dementia Res Inst, London, England Kings Coll London, Dept Basic & Clin Neurosci, Maurice Wohl Clin Neurosci Inst, Inst Psychiat Psychol & Neurosci, London, England Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USAIsaacs, Adrian论文数: 0 引用数: 0 h-index: 0机构: UCL, UK Dementia Res Inst, London, England UCL, Queen Sq Inst Neurol, Dept Neurodegenerat Dis, London, England UCL, Queen Sq Inst Neurol, UCL Queen Sq Motor Neuron Dis Ctr, London, England Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USACoyne, Alyssa N.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA Johns Hopkins Univ, Sch Med, Brain Sci Inst, Baltimore, MD 21205 USA