Phase 1/2 clinical trial of autologous hematopoietic stem and progenitor cell (HSPC) gene therapy for cystinosis

被引：0
|
作者：
Cherqui, Stephanie [1 ]
Ball, Edward [2 ]
Del Parigi, Angelo [3 ]
Kohn, Donald [4 ]
Barshop, Bruce [2 ]
机构：
[1] Univ Calif San Diego, Pediat, La Jolla, CA USA
[2] Univ Calif San Diego, La Jolla, CA USA
[3] AVROBIO, Cambridge, MA USA
[4] Univ Calif Los Angeles, Los Angeles, CA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2023年 / 138卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2022.107055
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
72
引用
收藏
页码：26 / 26
页数：1
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