Development of AAV-GBA1 Gene Replacement Therapy via Single-IV-Delivery with a Blood Brain Barrier Penetrant AAV Capsid

被引：0
|
作者：
Chung, Charlotte [1 ]
Retzlaff, Cassie [1 ]
Thompson, Jeff [1 ]
Bloedel, Alexis [1 ]
Bruce, Amy [1 ]
Ecker, Abigail [1 ]
Clement, Joseph [1 ]
Knoll, Elisabeth R. [1 ]
Ezell, Brian C. [1 ]
Hoffman, Brett [1 ]
Knox, Tatiana [1 ]
Nonnenmacher, Mathieu E. [1 ]
Moyer, Tyler [1 ]
Lin, Jing [1 ]
Grant, Kyle [1 ]
Paranjpe, Maneesha [1 ]
Pande, Nilesh [1 ]
Johnson, Amy [1 ]
Yao, Johnny [1 ]
Sadhu, Chanchal [1 ]
Carter, Todd A. [1 ]
机构：
[1] Voyager Therapeut, Cambridge, MA USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
695
引用
收藏
页码：347 / 347
页数：1
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