Long-term safety outcomes of eliglustat in patients with Gaucher disease: Prospective, multi-center, observational, post authorization safety sub-registry study

被引：0
|
作者：
Giraldo, Pilar [1 ]
Batsu, Isabela [2 ]
Accomando, Beverly [3 ]
Gaemers, Sebastiaan J. M. [4 ]
Cil, Sefika Uslu [3 ]
Gouyette, Najat [5 ]
Scarpa, Maurizio [6 ]
机构：
[1] Hosp Quironsalud, Zaragoza, Spain
[2] Sanofi Genzyme, Bridgewater, NJ USA
[3] Sanofi, Cambridge, MA USA
[4] Sanofi, Amsterdam, Netherlands
[5] Capgemini Behalf Sanofi, Chilly Mazarin, France
[6] Univ Hosp Udine, Udine, Italy
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2023.107844
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
105
引用
收藏
页数：1
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