Impact of Type of Hypomethylating Agent (HMA) Used on Outcomes of Patients (Pts) with Higher-Risk Myelodysplastic Syndromes/Neoplasms (HR-MDS) - a Large, Multicenter, Retrospective Analysis

被引:0
|
作者
Bewersdorf, Philipp [1 ,2 ]
Kewan, Tariq [3 ]
Blaha, Ondrej [4 ,5 ,6 ]
Stahl, Maximilian [7 ]
Al Ali, Najla H. [8 ]
DeZern, Amy E. [9 ]
Sekeres, Mikkael A. [10 ]
Uy, Geoffrey L. [11 ]
Carraway, Hetty E. [12 ]
Desai, Pinkal [13 ]
Griffiths, Elizabeth A. [14 ]
Stein, Eytan M. [15 ]
Brunner, Andrew M. [16 ]
McMahon, Christine M. [17 ]
Zeidner, Joshua F. [18 ]
Savona, Michael R. [19 ]
Stempel, Jessica M. [20 ]
Chandhok, Namrata Sonia [21 ]
Ramaswamy, Rahul [22 ]
Roboz, Gail J. [23 ]
Rolles, Benjamin [24 ]
Wang, Eunice S. [14 ]
Harris, Amyah C. [25 ]
Amaya, Maria L. [26 ]
Hawkins, Hayley [27 ]
Grenet, Justin [28 ]
Gurnari, Carmelo [29 ]
Shallis, Rory M. [30 ]
Xie, Zhuoer [31 ]
Maciejewski, Jaroslaw P. [29 ]
Sallman, David A. [31 ]
Della Porta, Matteo Giovanni [32 ]
Komrokji, Rami S. [8 ]
Zeidan, Amer M. [33 ,34 ]
机构
[1] Mem Sloan Kettering Canc Ctr, New York, NY USA
[2] Yale Univ, Sect Hematol, Dept Med, New Haven, CT USA
[3] Yale Univ, Sect Hematol, Dept Internal Med, New Haven, CT USA
[4] Yale Univ, Sch Publ Hlth, Dept Biostat, New Haven, CT USA
[5] Yale Univ, Sch Publ Hlth, Yale Ctr Analyt Sci, New Haven, CT USA
[6] Yale Univ, Yale Canc Ctr, New Haven, CT USA
[7] Dana Farber Inst, Boston, MA USA
[8] H Lee Moffitt Canc Ctr & Res Inst, Dept Malignant Hematol, Tampa, FL USA
[9] Johns Hopkins Univ, Baltimore, MD USA
[10] Univ Miami, Sylvester Canc Ctr, Miami, FL USA
[11] Washington Univ, Div Oncol, Sch Med, St Louis, MO USA
[12] Cleveland Clin, Taussig Canc Inst, Dept Hematol & Med Oncol, Leukemia Program, Cleveland, OH USA
[13] Weill Cornell Med, New York, NY USA
[14] Roswell Park Comprehens Canc Ctr, Buffalo, NY USA
[15] Mem Sloan Kettering Canc Ctr, Leukemia Serv, New York, NY USA
[16] Dana Farber Canc Inst, Div Hematol Oncol, Boston, MA USA
[17] Univ Colorado, Div Hematol, Sch Med, Aurora, CO USA
[18] Univ N Carolina, Lineberger Comprehens Canc Ctr, Chapel Hill, NC USA
[19] Vanderbilt Univ, Vanderbilt Ingram Canc Ctr, Med Ctr, Nashville, TN USA
[20] Yale Sch Med, Sect Hematol, Dept Internal Med, New Haven, CT USA
[21] Univ Miami, Div Hematol, Miller Sch Med, Sylvester Comprehens Canc Ctr, Miami, FL USA
[22] Washington Univ, St Louis, MO USA
[23] New York Presbyterian Hosp, New York, NY USA
[24] Harvard Med Sch, Brigham & Womens Hosp, Boston, MA USA
[25] Dana Farber Canc Inst, Boston, MA USA
[26] Univ Colorado, Div Hematol, Aurora, CO USA
[27] Vanderbilt Univ, Med Ctr, Nashville, TN USA
[28] Weill Cornell, New York, NY USA
[29] Cleveland Clin, Taussig Canc Inst, Dept Translat Hematol & Oncol Res, Cleveland, OH USA
[30] Yale Univ, Yale Sch Med, Sect Hematol, Dept Internal Med, New Haven, CT USA
[31] H Lee Moffitt Canc Inst, Tampa, FL USA
[32] IRCCS, Ctr Canc, Humanitas Res Hosp, Milan, Italy
[33] Yale Canc Ctr, Dept Internal Med, New Haven, CT USA
[34] Smilow Canc Hosp, New Haven, CT USA
关键词
D O I
10.1182/blood-2023-178728
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页数:8
相关论文
共 50 条
  • [21] Clinical Implications of TP53 Mutations/Allelic State in Patients (Pts) with Myelodysplastic Syndromes/Neoplasms (MDS) Treated with Hypomethylating Agents (HMA)- a Multicenter, Retrospective Analysis from the Validate Database
    Kewan, Tariq
    Bewersdorf, Jan Philipp
    Blaha, Ondrej
    Stahl, Maximilian
    Al Ali, Najla H.
    DeZern, Amy E.
    Sekeres, Mikkael A.
    Carraway, Hetty E.
    Desai, Pinkal
    Griffiths, Elizabeth A.
    Stein, Eytan M.
    Brunner, Andrew M.
    Amaya, Maria L.
    Zeidner, Joshua F.
    Savona, Michael R.
    Stempel, Jessica M.
    Chandhok, Namrata Sonia
    Cochran, Hunter
    Ramaswamy, Rahul
    Singh, Abhay
    Roboz, Gail J.
    Rolles, Benjamin
    Wang, Eunice S.
    Harris, Amyah C.
    Shallis, Rory M.
    Xie, Zhuoer
    Padron, Eric
    Maciejewski, Jaroslaw P.
    Della Porta, Matteo Giovanni
    Komrokji, Rami S.
    Sallman, David A.
    Zeidan, Amer M.
    BLOOD, 2023, 142
  • [22] Sabatolimab (MBG453) Combination Treatment Regimens for Patients (Pts) with Higher-Risk Myelodysplastic Syndromes (HR-MDS): The MDS Studies in the Stimulus Immuno-Myeloid Clinical Trial Program
    Zeidan, Amer M.
    Al-Kali, Aref
    Borate, Uma
    Cluzeau, Thomas
    DeZern, Amy E.
    Esteve, Jordi
    Giagounidis, Aristoteles
    Kobata, Krissy
    Lyons, Roger
    Platzbecker, Uwe
    Sallman, David A.
    Santini, Valeria
    Sanz, Guillermo
    Sekeres, Mikkael A.
    Wei, Andrew H.
    Xiao, Zhijian
    Van Hoef, Marlies
    Nourry-Boulot, Claire
    Sadek, Islam
    Bengoudifa, Bourras-Rezki
    Sachs, Carolin
    Sabo, John
    Garcia-Manero, Guillermo
    BLOOD, 2021, 138
  • [23] ECONOMIC IMPACT AND HEALTHCARE UTILIZATION IN PATIENTS WITH HIGHER-RISK MYELODYSPLASTIC SYNDROMES (HR-MDS) IN ROUTINE CLINICAL CARE IN THE UNITED STATES (US) - A CLAIMS DATABASE STUDY
    Bell, J.
    Galaznik, A.
    Farrelly, E.
    Blazer, M.
    Shih, H. -C.
    Raju, A.
    Ogbonnaya, A.
    Eaddy, M.
    Fram, R.
    Faller, D.
    HAEMATOLOGICA, 2017, 102 : 486 - 486
  • [24] TREATMENT PATTERNS IN PATIENTS WITH HIGHER-RISK MYELODYSPLASTIC SYNDROMES (HR-MDS) IN ROUTINE CLINICAL CARE IN THE UNITED STATES (US) - A CLAIMS DATABASE STUDY
    Bell, J.
    Galaznik, A.
    Farrelly, E.
    Blazer, M.
    Shih, H-C.
    Raju, A.
    Ogbonnaya, A.
    Eaddy, M.
    Fram, R.
    Faller, D.
    HAEMATOLOGICA, 2017, 102 : 491 - 492
  • [25] Genomic Profiling in Patients with Higher-Risk Myelodysplastic Syndrome (HR-MDS) Following HMA Failure: Baseline Results from the Inspire Study (04-30)
    Garcia-Manero, Guillermo
    Jonasova, Anna
    Luger, Selina M.
    Al-Kali, Aref
    Valcarcel, David
    Warlick, Erica D.
    Jedrzejczak, Wieslaw W.
    Diez-Campelo, Maria
    Zbyszewski, Patrick S.
    Cavanaugh, Christopher
    Woodman, Richard C.
    Fruchtman, Steven M.
    Takahashi, Koichi
    BLOOD, 2019, 134
  • [26] SYSTEMATIC REVIEW OF THERAPY USED IN HIGHER-RISK (HR) MYELODYSPLASTIC SYNDROMES (MDS) AND CHRONIC MYELOMONOCYTIC LEUKEMIA (CMML)
    Bell, J.
    Galaznik, A.
    Huelin, R.
    Stokes, M.
    Seal, B.
    Fram, R.
    Faller, D. V.
    LEUKEMIA RESEARCH, 2017, 55 : S80 - S81
  • [27] NOVEL PREDICTIVE INDICATORS IN PATIENTS WITH HIGHER-RISK MYELODYSPLASTIC NEOPLASMS (HR-MDS) TREATED WITH 5-AZACYTIDINE: CUMULATIVE DATA FROM THE HELLENIC MDS STUDY GROUP
    Kotsianidis, I.
    Hatzimichael, E.
    Pappa, V.
    Galanopoulos, A.
    Kourakli, A.
    Diamantopoulos, P.
    Papageorgiou, S.
    Liapis, K.
    Papadopoulos, V.
    Papoutselis, M.
    Bouchla, A.
    Georgoulis, V.
    Vassilakopoulos, T.
    Solomou, E.
    Dimou, M.
    Vassilopoulos, G.
    Vardi, A.
    Papaioannou, M.
    Pontikoglou, C.
    Anagnostopoulos, A.
    Panayiotidis, P.
    Kontopidou, F.
    Harchalakis, N.
    Adamopoulos, N.
    Ximeri, M.
    Zikos, P.
    Megalakaki, A.
    Repousis, P.
    Kotsopoulou, M.
    Dryllis, G.
    Tsoukanas, D.
    Kyrtsonis, M. -C.
    Poulakidas, E.
    Bouronikou, E.
    Delimpasis, S.
    Mparmparousi, D.
    Papadaki, H.
    Vyniou, N. A.
    Symeonidis, A.
    LEUKEMIA RESEARCH, 2023, 128
  • [28] Impact Of Magrolimab in Combination With Azacitidine on Red Blood Cells (RBCs) in Patients With Higher-Risk Myelodysplastic Syndromes (HR MDS)
    Chen, James
    Johnson, Lisa
    McKenna, Kelly
    Choi, Timothy
    Duan, Jiaqi
    Feng, Dongdong
    Tsai, Jonathan
    Garcia-Martin, Natalia
    Sompalli, Kavitha
    Maute, Roy
    Vyas, Paresh
    Majeti, Ravindra
    Takimoto, Chris
    Liu, Jie
    Ramsingh, Giridharan
    Chao, Mark
    Volkmer, Jens-Peter
    Weissman, Irving
    CLINICAL LYMPHOMA MYELOMA & LEUKEMIA, 2022, 22 : S317 - S318
  • [29] Impact Of The Achievement Of a Complete Cytogenetic Response (CCyR) On Outcome In Patients (pts) With Myelodysplastic Syndromes (MDS) Treated With Hypomethylating Agents (HMA)
    Jabbour, Elias
    Kantarjian, Hagop M.
    Qiao, Wei
    Strati, Paolo
    Khan, Navira F.
    Cortes, Jorge E.
    Hoehn, Daniela
    Hu, Jianhua
    Obrien, Susan
    Bryan, Jeffrey
    Prescott, Hillary
    DiNardo, Courtney D.
    Daver, Naval
    Kadia, Tapan M.
    Garcia-Manero, Guillermo
    BLOOD, 2013, 122 (21)
  • [30] PATIENT-CENTRIC CARE (PCC) IN HIGHER-RISK MYELODYSPLASTIC SYNDROMES (HR-MDS): A GLOBAL SYSTEMATIC LITERATURE REVIEW (SLR) AND GAP ANALYSIS
    Armstrong, E. P.
    Franic, D.
    Malone, D. C.
    Pham, S., V
    Hogea, C.
    VALUE IN HEALTH, 2023, 26 (06) : S334 - S334