In Vivo Genetic Eye Disease Correction Using Split AAV-Mediated Adenine Base Editing

被引：0

作者：

Sullivan, Jack ^{[1
]}

Muller, Alissa ^{[2
,3
]}

Schwarzer, Wibke ^{[2
,3
]}

Wang, Mantian ^{[2
,3
]}

Park-Windhol, Cindy ^{[1
]}

Hasler, Pascal ^{[3
]}

Moreau, Pierre-Henri ^{[4
]}

Azoulay, Thierry ^{[5
]}

Janeschitz-Kriegl, Lucas ^{[2
,3
]}

Szabo, Arnold ^{[6
]}

Scholl, Hendrik P. N. ^{[2
,3
]}

Roska, Botond ^{[2
,3
]}

Gyorgy, Bence ^{[2
,3
]}

Bryson, David I. ^{[1
]}

Ciaramella, Giuseppe ^{[1
]}

机构：

[1] Beam Therapeut, Cambridge, MA USA

[2] Inst Mol & Clin Ophthalmol Basel, Basel, Switzerland

[3] Univ Basel, Dept Ophthalmol, Basel, Switzerland

[4] Univ Strasbourg, SILABE, Niederhausbergen, France

[5] Clin Vet Agoravet, Strasbourg, France

[6] Semmelweis Univ, Dept Anat, Budapest, Hungary

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

308

引用

页码：168 / 168

页数：1

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