Combination of chemotherapy and all-trans retinoic acid for the treatment KMT2A-rearranged infant acute lymphoblastic leukemia. Results of the MLL-Baby trial

被引:2
|
作者
Fechina, Larisa [1 ,2 ]
Popov, Alexander [3 ]
Tsaur, Grigory [1 ,2 ,4 ]
Henze, Guenter [5 ]
Shorikov, Egor [6 ]
Makarova, Olga [1 ]
Khlebnikova, Olga [1 ]
Zhukova, Yulia [1 ]
Arakaev, Oleg [1 ,2 ]
Streneva, Olga [1 ,2 ]
Verzhbitskaya, Tatiana [1 ,2 ]
Riger, Tatiana [1 ,2 ]
Solodovnikov, Alexander [4 ]
Lapotentova, Elena [7 ]
Aleinikova, Olga [3 ,7 ]
Myakova, Natalia [3 ]
Boichenko, Elmira [8 ]
Kondratchik, Konstantin [9 ]
Nikonova, Olga [10 ]
Shapochnik, Alexander [11 ]
Goroshkova, Marina [12 ]
Ponomareva, Natalia [13 ]
Novichkova, Galina [3 ]
Karachunskiy, Alexander [3 ]
Roumiantsev, Alexander [3 ]
机构
[1] Reg Childrens Hosp, Ekaterinburg, Russia
[2] Res Inst Med Cell Technol, Ekaterinburg, Russia
[3] Natl Res & Clin Ctr Pediat Hematol Oncol & Immunol, Moscow, Russia
[4] Ural State Med Univ, Ekaterinburg, Russia
[5] Charite Univ Med Berlin, Dept Pediat Oncol Hematol, Berlin, Germany
[6] PET Technol Ctr Nucl Med, Ekaterinburg, Russia
[7] Belarussian Res Ctr Pediat Oncol Hematol & Immunol, Minsk, BELARUS
[8] City Childrens Hosp 1, St Petersburg, Russia
[9] Morozov Childrens Hosp, Moscow, Russia
[10] Reg Childrens Clin Hosp, Perm, Russia
[11] Orenburg Reg Clin Oncol Ctr, Orenburg, Russia
[12] Kuzbass Childrens Clin Hosp, Novokuznetsk, Russia
[13] Republican Childrens Hosp, Moscow, Russia
关键词
D O I
10.1038/s41375-023-02034-4
中图分类号
R73 [肿瘤学];
学科分类号
100214 ;
摘要
[No abstract available]
引用
收藏
页码:2276 / 2281
页数:6
相关论文
共 50 条
  • [21] GENOMIC DNA BREAKPOINTS IN MLL GENE AND TREATMENT OUTCOME IN INFANTS WITH ACUTE LYMPHOBLASTIC LEUKEMIA ENROLLED INTO MLL-BABY TRIAL
    Tsaur, G.
    Meyer, C.
    Popov, A.
    Kustanovich, A.
    Riger, T.
    Olshanskaya, Y.
    Matveeva, E.
    Fleischman, E.
    Sokova, O.
    Streneva, O.
    Saveliev, L.
    Marschalek, R.
    Solodovnikov, A.
    Shorikov, E.
    Fechina, L.
    PEDIATRIC BLOOD & CANCER, 2015, 62 : S212 - S212
  • [22] Minimal Residual Disease Monitoring by Quantification of Fusion Gene Transcripts In Infant with MLL-rearranged Acute Lymphoblastic Leukemia Treated by MLL-Baby Protocol
    Tsaur, Grigory
    Popov, Alexander
    Nasedkina, Tatyana
    Kalennik, Olga
    Kustanovich, Anatoly
    Aleinikova, Olga
    Riger, Tatyana
    Yakovleva, Yulia
    Iyanova, Anna
    Shorikov, Egor
    Saveliev, Leonid
    Fechina, Larisa
    BLOOD, 2010, 116 (21) : 1126 - 1126
  • [23] Phase 2 trial of the histone deacetylase inhibitor valproic acid as a monotherapy or in combination with all-trans retinoic acid in 24 patients with acute myeloid leukemia.
    Kuendgen, A
    Strupp, C
    Hildebrandt, B
    Knipp, S
    Junge, B
    Haas, R
    Germing, U
    Gattermann, N
    BLOOD, 2004, 104 (11) : 501A - 501A
  • [24] Genetic characteristics and treatment outcome in infants with KMT2A germline B-cell precursor acute lymphoblastic leukemia: Results of MLL-Baby protocol
    Popov, Alexander
    Tsaur, Grigory
    Permikin, Zhan
    Henze, Guenter
    Verzhbitskaya, Tatiana
    Plekhanova, Olga
    Nokhrina, Ekaterina
    Valochnik, Alena
    Sibiryakov, Petr
    Zerkalenkova, Elena
    Olshanskaya, Yulia
    Gindina, Tatiana
    Movchan, Liudmila
    Shorikov, Egor
    Streneva, Olga
    Khlebnikova, Olga
    Makarova, Olga
    Arakaev, Oleg
    Boichenko, Elmira
    Kondratchik, Konstantin
    Ponomareva, Natalia
    Lapotentova, Elena
    Aleinikova, Olga
    Miakova, Natalia
    Novichkova, Galina
    Karachunskiy, Alexander
    Fechina, Larisa
    PEDIATRIC BLOOD & CANCER, 2023, 70 (04)
  • [25] USE OF ALL-TRANS RETINOIC ACID IN THE TREATMENT OF ACUTE PROMYELOCYTIC LEUKEMIA
    HUANG, ME
    YE, YC
    CHEN, SR
    CHAI, JR
    LU, JX
    ZHOA, L
    GU, LJ
    WANG, ZY
    BLOOD, 1988, 72 (02) : 567 - 572
  • [26] All-trans retinoic acid for the treatment of acute promyelocytic leukemia in pregnancy
    Incerpi, MH
    Miller, DA
    Posen, R
    Byrne, JD
    OBSTETRICS AND GYNECOLOGY, 1997, 89 (05): : 826 - 828
  • [27] All-trans retinoic acid in the treatment of pediatric acute promyelocytic leukemia
    Masetti, Riccardo
    Vendemini, Francesca
    Zama, Daniele
    Biagi, Carlotta
    Gasperini, Pietro
    Pession, Andrea
    EXPERT REVIEW OF ANTICANCER THERAPY, 2012, 12 (09) : 1191 - 1204
  • [28] All-trans retinoic acid:: Treatment and toxicity in acute promyelocytic leukemia
    Ayyildiz, O
    Aybak, M
    Tiftik, N
    Müftüoglu, E
    12TH MEDITERRANEAN CONGRESS OF CHEMOTHERAPY, 2000, : 149 - 153
  • [29] All-trans retinoic acid - Progress in treatment of acute promyelocytic leukemia
    Lengfelder, E
    Hehlmann, R
    ONKOLOGIE, 1997, 20 (02): : 122 - 124
  • [30] Preclinical efficacy of azacitidine and venetoclax for infant KMT2A-rearranged acute lymphoblastic leukemia reveals a new therapeutic strategy
    Cheung, Laurence C.
    Aya-Bonilla, Carlos
    Cruickshank, Mark N.
    Chiu, Sung K.
    Kuek, Vincent
    Anderson, Denise
    Chua, Grace-Alyssa
    Singh, Sajla
    Oommen, Joyce
    Ferrari, Emanuela
    Hughes, Anastasia M.
    Ford, Jette
    Kunold, Elena
    Hesselman, Maria C.
    Post, Frederik
    Faulk, Kelly E.
    Breese, Erin H.
    Guest, Erin M.
    Brown, Patrick A.
    Loh, Mignon L.
    Lock, Richard B.
    Kees, Ursula R.
    Jafari, Rozbeh
    Malinge, Sebastien
    Kotecha, Rishi S.
    LEUKEMIA, 2023, 37 (01) : 61 - 71