Results from a 36-Week Open-Label Study of Recombinant Human Growth Hormone and Testosterone in Facioscapulohumeral Muscular Dystrophy (FSHD)

被引:0
|
作者
Heatwole, Chad [1 ]
Luebbe, Elizabeth [1 ]
Hamel, Johanna [1 ]
Mongiovi, Philip [1 ]
Ciafaloni, Emma [1 ]
Dilek, Nuran [1 ]
Martens, William [1 ]
Weber, David [2 ]
Hani, Rashid [1 ]
Allen, Jamie [1 ]
Smith, Claire [1 ]
Howell, Samantha [1 ]
Rosero, Spencer [1 ]
Eichinger, Katy [1 ]
Baker, Linday [1 ]
Dekdebrun, Jeanne [1 ]
Hilbert, Jim [1 ]
Varma, Anika [1 ]
McDermott, Michael [1 ]
Thornton, Charles [1 ]
Moxley, Richard [1 ]
机构
[1] Univ Rochester Med Ctr, Rochester, NY USA
[2] Childrens Hosp Philadelphia, Philadelphia, PA USA
关键词
D O I
10.1212/WNL.0000000000202958
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
S48.009
引用
收藏
页数:5
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