Therapeutic Genome Editing for Tay-Sachs Disease with a Simple CRISPR-Cas9 System

被引：0
|
作者：
Hung, Joshua E. [1 ,2 ]
Brewer, Reid A. [1 ,2 ]
Ivakine, Evgueni A. [1 ,2 ]
机构：
[1] Hosp Sick Children, Genet & Genome Biol Program, Toronto, ON, Canada
[2] Univ Toronto, Dept Physiol, Toronto, ON, Canada
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1364
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收藏
页码：643 / 644
页数：2
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