Experiences of parents/caregivers of children in the ASPIRO X-Linked myotubular myopathy (XLMTM) gene therapy clinical trial: a qualitative study

被引：0
|
作者：
Juando-Prats, C. [1 ]
Hodwitz, K. [1 ]
Kenneally, N. [2 ]
Alfano, L. [3 ]
Sarazen, M. [4 ]
Coats, J. [4 ]
机构：
[1] St Michaels Hosp, Li Ka Shing Knowledge Inst, Appl Hlth Res Ctr, Unity Hlth Toronto, Toronto, ON, Canada
[2] MacEwan Univ, Dept Human Serv & Early Learning, Early Childhood Curriculum Studies, Edmonton, AB, Canada
[3] Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA
[4] Astellas Gene Therapies, San Francisco, CA USA
来源：
NEUROMUSCULAR DISORDERS | 2023年 / 33卷
关键词：
D O I：
10.1016/j.nmd.2023.07.033
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P52
引用
收藏
页码：S71 / S71
页数：1
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