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- [21] Development and evaluation of a patient-reported outcome measure specific for Gaucher disease with or without neurological symptoms in JapanORPHANET JOURNAL OF RARE DISEASES, 2024, 19 (01)Narita, Aya论文数: 0 引用数: 0 h-index: 0机构: Tottori Univ, Div Child Neurol, Inst Neurol Sci, Fac Med, Yonago, Japan Tottori Univ, Div Child Neurol, Inst Neurol Sci, Fac Med, Yonago, JapanKoto, Yuta论文数: 0 引用数: 0 h-index: 0机构: Osaka Aoyama Univ, Fac Hlth Sci, Sch Nursing, Osaka, Japan Tottori Univ, Div Child Neurol, Inst Neurol Sci, Fac Med, Yonago, JapanNoto, Shinichi论文数: 0 引用数: 0 h-index: 0机构: Niigata Univ Hlth & Welf, Dept Rehabil, Niigata, Japan Tottori Univ, Div Child Neurol, Inst Neurol Sci, Fac Med, Yonago, JapanOkada, Masafumi论文数: 0 引用数: 0 h-index: 0机构: IQVIA Solut Japan KK, Real World Evidence Solut & HEOR, Tokyo, Japan Tottori Univ, Div Child Neurol, Inst Neurol Sci, Fac Med, Yonago, JapanOno, Midori论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Japan Med Off, Tokyo, Japan Tottori Univ, Div Child Neurol, Inst Neurol Sci, Fac Med, Yonago, JapanBaba, Terumi论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Japan Med Off, Tokyo, Japan Tottori Univ, Div Child Neurol, Inst Neurol Sci, Fac Med, Yonago, JapanSagara, Rieko论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Japan Med Off, Tokyo, Japan Tottori Univ, Div Child Neurol, Inst Neurol Sci, Fac Med, Yonago, JapanSakai, Norio论文数: 0 引用数: 0 h-index: 0机构: Osaka Univ, Grad Sch Med, Div Hlth Sci, Child Healthcare & Genet Sci Lab, 1-7 Yamadaoka, Suita, Osaka 5650871, Japan Tottori Univ, Div Child Neurol, Inst Neurol Sci, Fac Med, Yonago, Japan
- [22] Development and evaluation of a patient-reported outcome measure specific for Gaucher disease with or without neurological symptoms in JapanOrphanet Journal of Rare Diseases, 19Aya Narita论文数: 0 引用数: 0 h-index: 0机构: Tottori University,Division of Child Neurology, Faculty of Medicine, Institute of Neurological ScienceYuta Koto论文数: 0 引用数: 0 h-index: 0机构: Tottori University,Division of Child Neurology, Faculty of Medicine, Institute of Neurological ScienceShinichi Noto论文数: 0 引用数: 0 h-index: 0机构: Tottori University,Division of Child Neurology, Faculty of Medicine, Institute of Neurological ScienceMasafumi Okada论文数: 0 引用数: 0 h-index: 0机构: Tottori University,Division of Child Neurology, Faculty of Medicine, Institute of Neurological ScienceMidori Ono论文数: 0 引用数: 0 h-index: 0机构: Tottori University,Division of Child Neurology, Faculty of Medicine, Institute of Neurological ScienceTerumi Baba论文数: 0 引用数: 0 h-index: 0机构: Tottori University,Division of Child Neurology, Faculty of Medicine, Institute of Neurological ScienceRieko Sagara论文数: 0 引用数: 0 h-index: 0机构: Tottori University,Division of Child Neurology, Faculty of Medicine, Institute of Neurological ScienceNorio Sakai论文数: 0 引用数: 0 h-index: 0机构: Tottori University,Division of Child Neurology, Faculty of Medicine, Institute of Neurological Science
- [23] The Huntington's Disease Health Index: Initial Evaluation of a Disease-Specific Patient Reported Outcome MeasureJOURNAL OF HUNTINGTONS DISEASE, 2022, 11 (02) : 217 - 226Brumfield, Olivia S.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Ctr Hlth Technol, Rochester, NY USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USAZizzi, Christine E.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Ctr Hlth Technol, Rochester, NY USA Princeton Univ, Sch Publ & Int Affairs, Princeton, NJ 08544 USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USADilek, Nuran论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Dept Neurol, Rochester, NY USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USAAlexandrou, Danae G.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Ctr Hlth Technol, Rochester, NY USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USAGlidden, Alistair M.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Ctr Hlth Technol, Rochester, NY USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USA论文数: 引用数: h-index:机构:Weinstein, Jennifer论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Ctr Hlth Technol, Rochester, NY USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USASeabury, Jamison论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Ctr Hlth Technol, Rochester, NY USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USAKaat, Aaron论文数: 0 引用数: 0 h-index: 0机构: Northwestern Univ, Feinberg Sch Med, Dept Med Sci, Chicago, IL 60611 USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USAMcDermott, Michael P.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Dept Neurol, Rochester, NY USA Univ Rochester, Dept Biostat & Computat Biol, Rochester, NY USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USADorsey, E. Ray论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Ctr Hlth Technol, Rochester, NY USA Univ Rochester, Dept Neurol, Rochester, NY USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USAHeatwole, Chad R.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Ctr Hlth Technol, Rochester, NY USA Univ Rochester, Dept Neurol, Rochester, NY USA Univ Rochester, Ctr Hlth Technol, Rochester, NY USA
- [24] Development of a Novel Adult Congenital Heart Disease-Specific Patient-Reported Outcome MetricJOURNAL OF THE AMERICAN HEART ASSOCIATION, 2020, 9 (11):Cedars, Ari M.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USAKo, Jong Mi论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USAJohn, Anitha S.论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl Med Ctr, Dept Cardiol, Washington, DC 20010 USA Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USAVittengl, Jeffrey论文数: 0 引用数: 0 h-index: 0机构: Truman State Univ, Dept Psychol, Kirksville, MO USA Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USAStefanescu-Schmidt, Ada C.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Cardiol, Boston, MA 02114 USA Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USAJarrett, Robin B.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Dept Psychiat, Dallas, TX 75390 USA Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USAKutty, Shelby论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Sch Med, Dept Pediat Cardiol, Baltimore, MD USA Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USASpertus, John A.论文数: 0 引用数: 0 h-index: 0机构: Mid Amer Heart Inst, Dept Cardiol, Kansas City, KS USA Univ Texas Southwestern Med Ctr Dallas, Div Cardiol, Dept Internal Med, Dallas, TX 75390 USA
- [25] Measuring health-related quality of life in cardiovascular disease using a novel patient-centred and disease-specific patient-reported outcome measureINTERNATIONAL JOURNAL OF CARDIOLOGY CARDIOVASCULAR RISK AND PREVENTION, 2025, 24论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Groot, Hilde E.论文数: 0 引用数: 0 h-index: 0机构: Univ Groningen, Univ Med Ctr Groningen, Dept Cardiol, Groningen, Netherlands Univ Groningen, Univ Med Ctr Groningen, Dept Cardiol, Groningen, NetherlandsKrabbe, Paul F. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Groningen, Univ Med Ctr Groningen, Dept Epidemiol, Groningen, Netherlands Chateau Sante, Zeist, Netherlands Univ Groningen, Univ Med Ctr Groningen, Dept Cardiol, Groningen, Netherlands论文数: 引用数: h-index:机构:
- [26] Development of interim patient-reported outcome measures for the assessment of ulcerative colitis disease activity in clinical trialsALIMENTARY PHARMACOLOGY & THERAPEUTICS, 2015, 42 (10) : 1200 - 1210Jairath, V.论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, England Oxford Clin Trials Res Unit, Oxford, England Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, EnglandKhanna, R.论文数: 0 引用数: 0 h-index: 0机构: Univ Western Ontario, Robarts Clin Trials, London, ON, Canada Univ Western Ontario, Dept Med, London, ON, Canada Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, EnglandZou, G. Y.论文数: 0 引用数: 0 h-index: 0机构: Univ Western Ontario, Robarts Clin Trials, London, ON, Canada Univ Western Ontario, Dept Epidemiol & Biostat, London, ON, Canada Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, EnglandStitt, L.论文数: 0 引用数: 0 h-index: 0机构: Univ Western Ontario, Robarts Clin Trials, London, ON, Canada Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, EnglandMosli, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Western Ontario, Robarts Clin Trials, London, ON, Canada Univ Western Ontario, Dept Med, London, ON, Canada King Abdulaziz Univ, Dept Med, Jeddah 21413, Saudi Arabia Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, EnglandVandervoort, M. K.论文数: 0 引用数: 0 h-index: 0机构: Univ Western Ontario, Robarts Clin Trials, London, ON, Canada Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, EnglandD'Haens, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Western Ontario, Robarts Clin Trials, London, ON, Canada Univ Amsterdam, Acad Med Ctr, Ctr Inflammatory Bowel Dis, NL-1105 AZ Amsterdam, Netherlands Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, EnglandSandborn, W. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Western Ontario, Robarts Clin Trials, London, ON, Canada Univ Calif San Diego, Div Gastroenterol, La Jolla, CA 92093 USA Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, EnglandFeagan, B. G.论文数: 0 引用数: 0 h-index: 0机构: Univ Western Ontario, Robarts Clin Trials, London, ON, Canada Univ Western Ontario, Dept Med, London, ON, Canada Univ Western Ontario, Dept Epidemiol & Biostat, London, ON, Canada Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, EnglandLevesque, B. G.论文数: 0 引用数: 0 h-index: 0机构: Univ Western Ontario, Robarts Clin Trials, London, ON, Canada Univ Calif San Diego, Div Gastroenterol, La Jolla, CA 92093 USA Univ Oxford, Nuffield Dept Med, Translat Gastroenterol Unit, Oxford, England
- [27] Development of a Novel Hematological Malignancy Specific Patient-Reported Outcome Measure (HM-PRO): Content ValidityFRONTIERS IN PHARMACOLOGY, 2020, 11Goswami, Pushpendra论文数: 0 引用数: 0 h-index: 0机构: Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, England Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandOliva, Esther N.论文数: 0 引用数: 0 h-index: 0机构: Grande Osped Metropolitano, Haematol Unit, Reggio Di Calabria, Italy Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandIonova, Tatyana论文数: 0 引用数: 0 h-index: 0机构: St Petersburg State Univ, Med Ctr, St Petersburg, Russia St Petersburg State Univ, Multinatl Ctr Qual Life Res, St Petersburg, Russia Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandElse, Roger论文数: 0 引用数: 0 h-index: 0机构: Patient Res Partner, Milton Keynes, Bucks, England Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandKell, Jonathan论文数: 0 引用数: 0 h-index: 0机构: Cardiff & Vale Univ Hlth Board, Cardiff, Wales Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandFielding, Adele K.论文数: 0 引用数: 0 h-index: 0机构: UCL, Canc Inst, London, England Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandJennings, Daniel M.论文数: 0 引用数: 0 h-index: 0机构: Royal Surrey NHS Fdn Trust, Guildford, Surrey, England Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandKarakantza, Marina论文数: 0 引用数: 0 h-index: 0机构: Leeds Teaching Hosp NHS Trust, Leeds, W Yorkshire, England Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandAl-Ismail, Saad论文数: 0 引用数: 0 h-index: 0机构: ABM Univ Hlth Board, Singleton Hosp, Swansea, W Glam, Wales Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandCollins, Graham P.论文数: 0 引用数: 0 h-index: 0机构: Oxford Univ Hosp NHS Fdn Trust, Oxford, England Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandMcConnell, Stewart论文数: 0 引用数: 0 h-index: 0机构: Leeds Teaching Hosp NHS Trust, Leeds, W Yorkshire, England Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, EnglandLangton, Catherine论文数: 0 引用数: 0 h-index: 0机构: Leeds Teaching Hosp NHS Trust, Leeds, W Yorkshire, England Univ Hertfordshire, Sch Life & Med Sci, Hatfield, Herts, England论文数: 引用数: h-index:机构:
- [28] Patient perceptions of health-related quality of life in giant cell arteritis: international development of a disease-specific patient-reported outcome measureRHEUMATOLOGY, 2021, 60 (10) : 4671 - 4680Robson, Joanna C.论文数: 0 引用数: 0 h-index: 0机构: Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, England Univ Hosp & Weston Bristol NHS Fdn Trust, Bristol Royal Infirm, Bristol, Avon, England Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, EnglandAlmeida, Celia论文数: 0 引用数: 0 h-index: 0机构: Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, England Univ Hosp & Weston Bristol NHS Fdn Trust, Bristol Royal Infirm, Bristol, Avon, England Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, EnglandDawson, Jill论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Nuffield Dept Populat Hlth HSRU, Oxford, England Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, EnglandBromhead, Alison论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp & Weston Bristol NHS Fdn Trust, Bristol Royal Infirm, Bristol, Avon, England Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, EnglandDures, Emma论文数: 0 引用数: 0 h-index: 0机构: Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, England Univ Hosp & Weston Bristol NHS Fdn Trust, Bristol Royal Infirm, Bristol, Avon, England Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, EnglandGuly, Catherine论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp & Weston Bristol NHS Fdn Trust, Bristol Royal Infirm, Bristol, Avon, England Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, EnglandHoon, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Univ Adelaide, Sch Publ Hlth, Adelaide, SA, Australia Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, EnglandMackie, Sarah论文数: 0 引用数: 0 h-index: 0机构: Univ Leeds, Leeds Biomed Res Ctr, Leeds Inst Rheumat & Musculoskeletal Med, NIHR Natl Inst Hlth Res, Leeds, W Yorkshire, England Leeds Teaching Hosp NHS Natl Hlth Serv Trust, Leeds, W Yorkshire, England Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, England论文数: 引用数: h-index:机构:Pauling, John论文数: 0 引用数: 0 h-index: 0机构: Royal Natl Hosp Rheumat Dis, Dept Rheumatol, Bath, Avon, England Univ Bath, Dept Pharm & Pharmacol, Bath, Avon, England Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, EnglandHill, Catherine论文数: 0 引用数: 0 h-index: 0机构: Univ Adelaide, Sch Publ Hlth, Adelaide, SA, Australia Queen Elizabeth Hosp, Rheumatol Unit, Woodville, SA, Australia Royal Adelaide Hosp, Rheumatol Unit, Adelaide, SA, Australia Univ West England, Ctr Hlth & Clin Res, Bristol, Avon, England
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- [30] Development and validation of Gaucher disease type 1 (GD1)-specific patient-reported outcome measures (PROMs) for clinical monitoring and for clinical trialsORPHANET JOURNAL OF RARE DISEASES, 2022, 17 (01)Elstein, Deborahy论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Int AG, Zurich, Switzerland Takeda Pharmaceut Int AG, Zurich, SwitzerlandBelmatoug, Nadia论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Assistance Publ Hop Paris Nord, Paris, France Takeda Pharmaceut Int AG, Zurich, Switzerland论文数: 引用数: h-index:机构:Goker-Alpan, Ozlem论文数: 0 引用数: 0 h-index: 0机构: O&O Alpan LLC, Lysosomal Disorders Unit, Fairfax, VA USA O&O Alpan LLC, Ctr Clin Trials, Fairfax, VA USA Takeda Pharmaceut Int AG, Zurich, SwitzerlandHughes, Derralynn A.论文数: 0 引用数: 0 h-index: 0机构: Royal Free London NHS Fdn Trust, London, England Takeda Pharmaceut Int AG, Zurich, SwitzerlandSchwartz, Ida Vanessa D.论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio Grande do Sul, Dept Genet, Med Genet Serv HCPA, Porto Alegre, Brazil Takeda Pharmaceut Int AG, Zurich, SwitzerlandWeinreb, Neal论文数: 0 引用数: 0 h-index: 0机构: Univ Miami, Miller Sch Med, Miami, FL 33136 USA Takeda Pharmaceut Int AG, Zurich, SwitzerlandBonner, Nicola论文数: 0 引用数: 0 h-index: 0机构: Adelphi Values, Bollington, England Takeda Pharmaceut Int AG, Zurich, SwitzerlandPanter, Charlotte论文数: 0 引用数: 0 h-index: 0机构: Adelphi Values, Bollington, England Takeda Pharmaceut Int AG, Zurich, SwitzerlandFountain, Donna论文数: 0 引用数: 0 h-index: 0机构: PHMR, London, England Takeda Pharmaceut Int AG, Zurich, SwitzerlandLenny, Andrew论文数: 0 引用数: 0 h-index: 0机构: PHMR, London, England Takeda Pharmaceut Int AG, Zurich, SwitzerlandLongworth, Louise论文数: 0 引用数: 0 h-index: 0机构: PHMR, London, England Takeda Pharmaceut Int AG, Zurich, SwitzerlandMiller, Rachael论文数: 0 引用数: 0 h-index: 0机构: PHMR, London, England Takeda Pharmaceut Int AG, Zurich, SwitzerlandShah, Koonal论文数: 0 引用数: 0 h-index: 0机构: PHMR, London, England Takeda Pharmaceut Int AG, Zurich, SwitzerlandSchenk, Jorn论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Int AG, Zurich, Switzerland Takeda Pharmaceut Int AG, Zurich, SwitzerlandSen, Rohini论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Cambridge, MA USA Takeda Pharmaceut Int AG, Zurich, SwitzerlandZimran, Ari论文数: 0 引用数: 0 h-index: 0机构: Shaare Zedek Med Ctr, Gaucher Unit, Jerusalem, Israel Hebrew Univ Jerusalem, Hadassah Med Sch, Jerusalem, Israel Takeda Pharmaceut Int AG, Zurich, Switzerland