Rational Engineering of Novel Synthetic Promoters for Specific AAV-Delivered GRN Expression in the CNS

被引：0

作者：

Tome, Jacob M. ^{[1
]}

Al-Asadi, Hussein ^{[1
]}

Shannon, Sandra B. ^{[1
]}

Kall, Stephanie R. ^{[1
]}

Koday, Michael A. ^{[1
]}

Edwards, Samantha R. ^{[1
]}

Bussema, Lillian J. ^{[1
]}

Johnstone, Timothy G. ^{[1
]}

Jiang, Yue ^{[1
]}

Wang, Jonathan H. ^{[1
]}

Laing, Robyn J. ^{[1
]}

Chadwick, Eric M. ^{[1
]}

Hause, Ronald James ^{[1
]}

Briggs, Adrian W. ^{[1
]}

Sullivan, Richard T. ^{[1
]}

机构：

[1] Shape Therapeut Inc, Seattle, WA USA

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

379

引用

页码：203 / 203

页数：1

共 50 条

[41] Therapeutic Capacity of AAV-Delivered Muscle-Specific-Expressed Micro-Utrophin (ΔR4-R21/ΔCT) in mdx4cv Skeletal Muscles
Banks, Glen B.
Quynh Nguyen
Hauschka, Stephen D.
Chamberlain, Jeffrey S.
Odom, Guy L.
MOLECULAR THERAPY, 2016, 24 : S151 - S152
[42] The identification of novel promoters and terminators for protein expression and metabolic engineering applications in Kluyveromyces marxianus
Kumar, Pradeep
Sahoo, Debendra Kumar
Sharma, Deepak
METABOLIC ENGINEERING COMMUNICATIONS, 2021, 12
[43] Development of novel transciptionally responsive synthetic promoters for therapeutic gene expression during disease activity
Mohamed, Hodan
Chernajovsky, Yuti
Gould, David
HUMAN GENE THERAPY, 2013, 24 (05) : A36 - A36
[44] Development of novel transcriptionally responsive synthetic promoters for therapeutic gene expression during disease activity
Mohamed, Hodan
Chernajovsky, Yuti
Gould, David
HUMAN GENE THERAPY, 2014, 25 (05) : A8 - A8
[45] A novel expression assay system for fiber-specific promoters in developing cotton fibers
Hee Jin Kim
Marian Y. Williams
Barbara A. Triplett
Plant Molecular Biology Reporter, 2002, 20 : 7 - 18
[46] A novel expression assay system for fiber-specific promoters in developing cotton fibers
Kim, HJ
Williams, MY
Triplett, BA
PLANT MOLECULAR BIOLOGY REPORTER, 2002, 20 (01) : 7 - 18
[47] Small Nppa and Myl2 Promoters Are Sufficient to Maintain Chamber-specific Expression on an AAV9 Platform
Bilal, Alina
Blackwood, Erik
Thuerauf, Donna
Glembotski, Christopher
FASEB JOURNAL, 2020, 34
[48] Suppression of CNS APOE4 Expression by miRNAs Delivered by the S2 AAVrh.10 Capsid-Modified AAV Vector
Karan, Kalpita R.
Andrzejewski, Slawomir
Stiles, Katie M.
Hackett, Neil R.
Crystal, Ronald G.
HUMAN GENE THERAPY, 2024, 35 (21-22) : 904 - 916
[49] UPF1 delivered by novel expression-enhanced promoters protects cultured neurons in a genetic ALS model
Campbell, B. C.
Bekier, M.
Lettko, A.
Zamatkesh, M.
Lokhorst, D.
Van der Sanden, S.
Griffith, A.
Georgiadis, A.
Nguyen-Vu, B.
During, M.
Forbes, A.
Barmada, S. J.
Liu, C. F.
HUMAN GENE THERAPY, 2022, 33 (23-24) : A91 - A91
[50] Cell-Type Specific Oxytocin Gene Expression from AAV Delivered Promoter Deletion Constructs into the Rat Supraoptic Nucleus in vivo
Fields, Raymond L.
Ponzio, Todd A.
Kawasaki, Makoto
Gainer, Harold
PLOS ONE, 2012, 7 (02):

← 1 2 3 4 5 →