Lentiviral gene therapy for mucopolysaccharidosis type IVA

被引：0
|
作者：
Celik, Betul [1 ]
Rintz, Estera [2 ]
Nidhi, Fnu [3 ]
Khan, Shaukat [4 ]
Tomatsu, Shunji [5 ]
机构：
[1] Univ Delaware, Biol Sci, Newark, DE USA
[2] Univ Gdansk, Gdansk, Poland
[3] Univ Delaware, Newark, DE USA
[4] Nemours Alfred I Pont Hosp Children, Wilmington, DE USA
[5] Nemours Alfred I Pont Hosp Children, Biomed Res & Orthoped, Wilmington, DE USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2023年 / 138卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2022.107047
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
64
引用
收藏
页码：23 / 24
页数：2
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