Real-world safety and effectiveness of vosoritide: Results from an early access program in France

被引：0
|
作者：
Cormier-Daire, Valerie [1 ]
Edouard, Thomas [2 ]
Isidor, Bertrand [3 ]
Cohen, Shelda [4 ]
Mukherjee, Swati [4 ]
Pimenta, Jeanne [4 ]
Lhaneche, Leila [5 ]
Rossi, Massimiliano [6 ,7 ]
Schaefer, Elise [8 ]
Goodman, Erin [9 ]
Sigaudy, Sabine [10 ]
Baujat, Genevieve [11 ]
机构：
[1] Paris Ctr Univ, Imagine Inst, Necker Enfants Malad Hosp,INSERM,UMR 1163, Dept Clin Genet,Ctr Reference Constitut Bone Dis, Paris, France
[2] Toulouse Univ Hosp, Reference Ctr Rare Dis Calcium & Phosphate Metab, Paediat Res Unit,INSERM,U1301, ERN BOND,OSCAR Network,Childrens Hosp,RESTORE, Toulouse, France
[3] CHU Nantes, Nantes, France
[4] BioMarin UK Ltd, London, England
[5] BioMarin France, Paris, France
[6] Hosp Civils Lyon, Serv Genet, Lyon, France
[7] UCBL1, INSERM, U1028, CNRS,UMR5292,CRNL,GENDEV Team, Lyon, France
[8] Hop Hautepierre, CHU Strasbourg, Strasbourg, France
[9] BioMarin Pharmaceut Inc, Novato, CA USA
[10] Hop Timone Enfant, Dept Genet Med, Marseille, France
[11] Enfants Malad Hop Necker Enfants Malad, Hop Necker, Paris, France
来源：
HORMONE RESEARCH IN PAEDIATRICS | 2023年 / 96卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
RFC4.5
引用
收藏
页码：90 / 90
页数：1
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