[1] Salford Royal Fdn Trust, Adult Inherited Metab Dis, Salford, England
[2] Salford Royal NHS Fdn Trust, Adult Inherited Metab Dis, Salford, England
[3] St Marys Hosp, Paediat Inherited Metab Dis, Manchester, England
[4] Sheffield Teaching Hosp NHS Fdn Trust, Adult Inherited Metab Dis, Sheffield, England
[5] Royal Manchester Childrens Hosp, Blood & Marrow Transplant Unit, Manchester, England