Real-world data for patients with gestational age ≤35 weeks at birth treated with onasemnogene abeparvovec: results from the RESTORE Registry

被引：0
|
作者：
Finkel, R. [1 ]
Dabbous, O. [3 ]
Benguerba, K. [3 ]
Mumneh, N. [2 ]
Raju, D. [2 ]
Servais, L. [4 ,5 ,6 ]
机构：
[1] St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA
[2] Novartis Gene Therapies Inc, Bannockburn, IL USA
[3] Novartis Gene Therapies Switzerland GmbH, Rotkreuz, Switzerland
[4] Univ Oxford, Dept Paediat, MDUK Oxford Neuromuscular Ctr, Oxford, England
[5] Univ Liege, Dept Paediat, Neuromuscular Reference Ctr, Liege, Belgium
[6] Univ Hosp Liege, Liege, Belgium
来源：
NEUROMUSCULAR DISORDERS | 2023年 / 33卷
关键词：
D O I：
10.1016/j.nmd.2023.07.379
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P02
引用
收藏
页码：S162 / S162
页数：1
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