enOsCas12f1-mediated exon skipping for Duchenne muscular dystrophy therapy in humanized mouse model

被引：0

作者：

Jin, Ming ^{[1
,2
]}

Lin, Jiajia ^{[1
,2
]}

Zhang, Yu ^{[3
]}

Xiao, Qingquan ^{[3
]}

Kong, Xiangfeng ^{[3
]}

Zhang, Xiumei ^{[3
]}

Shao, Zhurui ^{[3
]}

Wang, Yin ^{[3
]}

Yu, Yuyang ^{[3
]}

Li, Jinjing ^{[1
,2
]}

Chen, Wan-Jin ^{[1
,2
]}

Li, Guoling ^{[3
]}

Yang, Hui ^{[3
,4
]}

Wang, Ning ^{[1
,2
]}

机构：

[1] Fujian Med Univ, Inst Neurosci, Dept Neurol, Fujian Key Lab Mol Neurol, Fuzhou 350004, Fujian, Peoples R China

[2] Fujian Med Univ, Affiliated Hosp 1, Inst Neurosci, Fujian Key Lab Mol Neurol,Inst Neurol, Fuzhou 350004, Fujian, Peoples R China

[3] HUIDAGENE Therapeut Co Ltd, Shanghai 200131, Peoples R China

[4] Chinese Acad Sci, Shanghai Inst Biol Sci, State Key Lab Neurosci,Key Lab Primate Neurobiol,C, Inst Neurosci, Shanghai 200031, Peoples R China

来源：

JOURNAL OF GENETICS AND GENOMICS | 2024年 / 51卷 / 02期

基金：

中国国家自然科学基金;

关键词：

D O I：

10.1016/j.jgg.2023.12.003

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

引用

页码：256 / 259

页数：4

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