The effectiveness of CFTR modulators in people with CF and rare mutations: A real-world study

被引：1
|
作者：
Hanger, Sofia [1 ]
Felton, Imogen [1 ]
Ukor, Emem-Fong [1 ]
Bowman, Elaine [1 ]
Caldwell, Clare [1 ]
Banya, Winston [2 ]
Madge, Susan [1 ]
Jones, Andrew L. [1 ]
Simmonds, Nicholas J. [1 ,3 ]
机构：
[1] Royal Brompton Hosp, Adult Cyst Fibrosis Ctr, London, England
[2] Royal Brompton Hosp, Res Off, Med Stat, London, England
[3] Imperial Coll London, Natl Heart & Lung Inst, London, England
来源：
PEDIATRIC PULMONOLOGY | 2024年 / 59卷 / 01期
关键词：
TEZACAFTOR-IVACAFTOR; CYSTIC-FIBROSIS;
D O I：
10.1002/ppul.26713
中图分类号：
R72 [儿科学];
学科分类号：
100202 ;
摘要：
引用
收藏
页码：221 / 224
页数：4
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